Duchenne muscular dystrophy (DMD) is a devastating, inherited muscle-wasting disorder caused by mutations in the DMD gene, leading to an absence of functional dystrophin protein. While current standards of care,…
The concept of “food as medicine” has gained significant traction in recent years, and for good reason: mounting evidence shows that nutrition is a powerful tool in both the prevention…
At the recent American Society of Clinical Oncology (ASCO) annual meeting, researchers unveiled remarkable long-term results for ciltacabtagene autoleucel (cilta-cel; Carvykti), a CAR T-cell therapy, in patients with heavily pretreated…
A groundbreaking advance in diabetes care has emerged from recent clinical research: a new cell therapy has successfully restored natural insulin production in 83% of participants living with diabetes. This…
Duchenne Muscular Dystrophy (DMD) is a severe, progressive neuromuscular disease that primarily affects boys, leading to muscle weakness, loss of ambulation, and premature death. Among therapeutic advances, ataluren has emerged…
June 2025 marked a month of significant progress in cancer care, as the FDA approved several new therapies and treatment combinations across a range of cancer types. As reported by…
The Accredited Duchenne Centers (ADC) Program, spearheaded by the World Duchenne Organization (WDO), is a pioneering global initiative designed to standardize and elevate care for individuals living with Duchenne Muscular…
KalVista Pharmaceuticals has achieved a significant milestone with the U.S. Food and Drug Administration’s (FDA) approval of its new oral therapy for hereditary angioedema (HAE), marking a breakthrough for patients…
A new milestone has been reached in the search for effective treatments for dry age-related macular degeneration (AMD), as the first patient has now been dosed in a clinical trial…
Fujifilm Corporation’s investigational therapy FF-10832 has received Orphan Drug Designation from the U.S. Food and Drug Administration (FDA) for the treatment of biliary tract cancer, according to a recent announcement…
The United States is experiencing its worst measles outbreak in decades, with cases rising sharply across multiple states. Health officials attribute this surge primarily to declining childhood vaccination rates, fueled…
A recent study has brought attention to the complex challenges faced by children with hidradenitis suppurativa (HS), a chronic and often painful skin condition. According to new research summarized by…
A new study has found that corticosteroids, commonly used to manage symptoms in lung cancer patients, may reduce the effectiveness of immunotherapy treatments. The research, highlighted by News-Medical.net, sheds light…
Recent research highlights a significant connection between eosinophilic gastrointestinal diseases (EGIDs) and atopic conditions such as asthma, eczema, and allergic rhinitis. EGIDs, which include disorders like eosinophilic esophagitis, gastritis, and…
Chronic obstructive pulmonary disease (COPD) remains one of the leading causes of illness and mortality worldwide, but new research highlights how its prevalence and overall disease burden vary considerably across…
Cogent Biosciences has announced new clinical trial results indicating that its drug BEZUCLASTINIB offers promising benefits for patients with indolent systemic mastocytosis (ISM), a rare and chronic disorder characterized by…
For most families, a sunny day is a source of joy, but for the family of five-year-old Evie-Rose, sunlight brings distress and fear. As was reported in the Scottish Sun,…
Recent research outlined by Medical Xpress offers a deeper understanding of why CDK4/6 inhibitors, a class of drugs widely used to treat certain cancers, sometimes fail to deliver lasting benefits.…
Go here to read Part 1, Part 2, Part 3, and Part 4 of this series provided by TREND Community about Prader-Willi Syndrome. On March 5, 2025, TREND Community released its…
The Vancouver Island community has come together in an emotional show of support for nine-year-old Charleigh Pollock after news broke that the B.C. government is discontinuing coverage of the only…
A groundbreaking development in respiratory medicine has emerged with the launch of a first-of-its-kind inhaler designed for conditions beyond the traditional scope of asthma and chronic obstructive pulmonary disease (COPD). …
A recent research article in ScienceDirect.com details a breakthrough in visualizing the rapid, complex movements of proteins using high-speed atomic force microscopy (HS-AFM). This cutting-edge imaging technology allows scientists to…
A recent case report has brought attention to a rare but potentially life-threatening cause of heart attack: spontaneous coronary artery dissection (SCAD) in a young woman without classic risk factors…
Madrigal Pharmaceuticals is making significant strides in its mission to address metabolic dysfunction-associated steatohepatitis (MASH), as the company’s lead drug, REZDIFFRA, edges closer to regulatory approval in the European Union.…
A recently published case report has shed light on an uncommon cause of abdominal pain in adults: small bowel intussusception due to a benign tumor known as a lipoma. As…
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