Benign Congenital Hypotonia and Other Rare Conditions: A Patient Story
Written by Kathleen Leatherbury Hi, I'd like to share my story. In hopes of 2 things. To find help and to hopefully help others. I apologize in advance, as this…
Written by Kathleen Leatherbury Hi, I'd like to share my story. In hopes of 2 things. To find help and to hopefully help others. I apologize in advance, as this…
A recent article in the publication CheckOrphan announced encouraging results of a long term extension study sponsored by Ultragenyx involving UX007 (triheptanoin) in patients with long-chain fatty acid oxidation disorders…