Hemoglobinopathy Archives - Patient Worthy

The World’s First Editing of DNA in Humans Using CRISPR to Treat Leber Congenital Amaurosis

Post author:Rose Duesterwald
Post published:August 19, 2019
Post category:Hemoglobinopathy Leber Congenital Amaurosis Retinitis pigmentosa

Allergan plc, a leading global pharmaceutical company, and its partner, Editas Medicine, Inc. have been given the green light for a clinical trial designed to treat patients with severe…

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The World’s First Editing of DNA in Humans Using CRISPR to Treat Leber Congenital Amaurosis

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