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Pyruvate kinase deficiency

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Mitapivat Beneficial for PKD, Study Shows
Photo courtesy of Towfiqu Barbhuiya on Unsplash

Mitapivat Beneficial for PKD, Study Shows

  • Post author:Jessica Lynn
  • Post published:June 13, 2022
  • Post category:Pyruvate kinase deficiency

Earlier this year, the U.S. Food and Drug Administration (FDA) approved mitapivat (PYRUKYND) for the treatment of patients with hemolytic anemia due to pyruvate kinase deficiency (PKD). According to 2…

Continue Reading Mitapivat Beneficial for PKD, Study Shows
PK Deficiency Treatment Called Pyrukynd is Now FDA Approved

PK Deficiency Treatment Called Pyrukynd is Now FDA Approved

  • Post author:Trudy Horsting
  • Post published:March 1, 2022
  • Post category:Pyruvate kinase deficiency

The FDA has recently approved a treatment called Pyrukynd as a therapeutic option for hemolytic anemia disorder sparked by pyruvate kinase deficiency. Hemolytic anemia is a condition where red blood…

Continue Reading PK Deficiency Treatment Called Pyrukynd is Now FDA Approved
PYRUKYND Approved in US for PK Deficiency
source: pixabay.com

PYRUKYND Approved in US for PK Deficiency

  • Post author:Jessica Lynn
  • Post published:February 23, 2022
  • Post category:Pyruvate kinase deficiency

Prior to February 2022, there were no approved disease-modifying therapies for those with pyruvate kinase (PK) deficiency. However, this has recently changed! According to a news release from biopharmaceutical company…

Continue Reading PYRUKYND Approved in US for PK Deficiency
New Data Available on RP-L301 for Pyruvate Kinase Deficiency 
qimono / Pixabay

New Data Available on RP-L301 for Pyruvate Kinase Deficiency 

  • Post author:Jessica Lynn
  • Post published:March 23, 2021
  • Post category:Pyruvate kinase deficiency

  Rocket Pharmaceuticals, Inc. ("Rocket") has dedicated its mission to developing gene therapy solutions for rare childhood conditions. Recently, the company shared the publication of preliminary data from a Phase…

Continue Reading New Data Available on RP-L301 for Pyruvate Kinase Deficiency 

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