Rare Disease

An Eleven-Year-Old Girl in Rowlett, Texas is Slated to Make Medical History

Rose Duesterwald - May 19, 2025
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Patient Worthy
2 hours ago
Patient Worthy

An 11-year-old girl in Texas is the first-ever person to be treated for an exceptionally rare genetic condition called NARS-1 disorder.

Read more with the link below:

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An 11-year-old girl in Texas is the first-ever person to be treated for an exceptionally rare genetic condition called NARS-1 disorder. Read more with the link below: https://bit.ly/43xpsUt
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Patient Worthy
2 days ago
Patient Worthy

May 17th is World NF Awareness Day! A reminder of the real impact neurofibromatosis has on thousands of lives. Awareness leads to understanding, and understanding drives progress. #worldNFawarenessday #EndNF #raredisease #shareyourstory

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May 17th is World NF Awareness Day! A reminder of the real impact neurofibromatosis has on thousands of lives. Awareness leads to understanding, and understanding drives progress. #WorldNFAwarenessDay #EndNF #RareDisease #ShareYourStory If youre interested in sharing your story, click here: https://bit.ly/3VuxFDV
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