Novel Gene Therapy Uses Brain Surgery to Achieve Results For Huntington’s Disease Patients, Part Two

As discussed in Part I of this article, a recent HDBUZZ publication featured a news item stating that due to several severe adverse events occurring during the initial AMT-130 trial…

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Experimental Gene Therapy Uses Brain Surgery to Achieve Results For Huntington’s Disease Patients, Part One
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Experimental Gene Therapy Uses Brain Surgery to Achieve Results For Huntington’s Disease Patients, Part One

When we ‘do the math’ it adds up to the novel AMT-130 gene therapy receiving positive results from uniQure’s clinical trial investigating a small group (N=4) of individuals who were…

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ICYMI: Swimmer’s 100km Swim Raised Huntington’s Disease Awareness
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ICYMI: Swimmer’s 100km Swim Raised Huntington’s Disease Awareness

HTT gene mutations cause Huntington’s disease, a rare and inherited neurological condition. Those with a family history of Huntington’s disease may choose to undergo genetic testing to learn more, though…

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Study of the Week: Study Reveals a Key Mechanism of Neurodegenerative Diseases
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Study of the Week: Study Reveals a Key Mechanism of Neurodegenerative Diseases

Welcome to Study of the Week from Patient Worthy. In this segment, we select a study we posted about from the previous week that we think is of particular interest…

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36th Annual HDSA Convention: Being Prepared for Huntington’s Disease Emergencies
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36th Annual HDSA Convention: Being Prepared for Huntington’s Disease Emergencies

Patient Worthy signed up to cover several sessions at the Huntington's Disease Society of America's (HDSA) 36th Annual Convention, which was held virtually this year. This event features informative presentations…

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Mouse Models Prove Success of Gene Therapy for the Treatment of Huntington’s Disease

Research has recently been published in Nature Communications that shows the success of a new gene therapy in the treatment of Huntington's Disease. This therapy, an adeno-associated virus-based gene therapy, was tested…

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Neuroscientists Use Genetic Screen to Identify Huntington’s Disease Drug Targets
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Neuroscientists Use Genetic Screen to Identify Huntington’s Disease Drug Targets

By Jodee Redmond from In The Cloud Copy Massachusetts Institute of Technology (MIT) researchers have recently announced they have identified hundreds of genes that are required for neuron survival. The…

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A Scientist Dedicated Her Life to Researching Huntington’s Disease Before Facing a Diagnosis Herself
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A Scientist Dedicated Her Life to Researching Huntington’s Disease Before Facing a Diagnosis Herself

According to a story from Yahoo News, Dr. Nancy Wexler spent around 20 years in Venezuela conducting pivotal research on a deadly rare genetic disorder: Huntington's disease. On Lake Maracaibo,…

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