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Breaking Ground: Palvella Therapeutics Completes Enrollment in Phase 2 TOIVA Trial for QTORIN™ Rapamycin in Cutaneous Venous Malformations

Breaking Ground: Palvella Therapeutics Completes Enrollment in Phase 2 TOIVA Trial for QTORIN™ Rapamycin in Cutaneous Venous Malformations

Palvella Therapeutics, Inc. has announced a key milestone in the development of therapies for rare genetic skin diseases: the completion of enrollment in its Phase 2 TOIVA trial of QTORIN™…

Continue Reading Breaking Ground: Palvella Therapeutics Completes Enrollment in Phase 2 TOIVA Trial for QTORIN™ Rapamycin in Cutaneous Venous Malformations
Diagnosis and management of sleep disorders in Prader-Willi syndrome

Diagnosis and management of sleep disorders in Prader-Willi syndrome

In our third installment from our series of reports provided by our partner TREND Community, we are bringing you several reports that analyze the effects of sleep disorders.  This week…

Continue Reading Diagnosis and management of sleep disorders in Prader-Willi syndrome
HYMPAVZI™: A New Era for Hemophilia Patients with Inhibitors

HYMPAVZI™: A New Era for Hemophilia Patients with Inhibitors

Pfizer has announced breakthrough Phase 3 results for HYMPAVZI™ (marstacimab), a once-weekly subcutaneous therapy that could redefine care for people with hemophilia A or B who have developed inhibitors, as…

Continue Reading HYMPAVZI™: A New Era for Hemophilia Patients with Inhibitors
Understanding the Patient Experience with Twice-Nightly Sodium Oxybate Therapy for Narcolepsy: A Social Listening Experiment

Understanding the Patient Experience with Twice-Nightly Sodium Oxybate Therapy for Narcolepsy: A Social Listening Experiment

In our third installment from our series of reports provided by our partner TREND Community, we are bringing you several reports that analyze the effects of sleep disorders.  This week…

Continue Reading Understanding the Patient Experience with Twice-Nightly Sodium Oxybate Therapy for Narcolepsy: A Social Listening Experiment
Regeneron and Alnylam’s RNA Drug Shows Promise for Rare Autoimmune Disease

Regeneron and Alnylam’s RNA Drug Shows Promise for Rare Autoimmune Disease

A new RNA-based drug from Regeneron Pharmaceuticals and Alnylam Pharmaceuticals has shown positive results in a late-stage clinical trial for generalized myasthenia gravis (gMG), a rare, chronic autoimmune disease that…

Continue Reading Regeneron and Alnylam’s RNA Drug Shows Promise for Rare Autoimmune Disease
Understanding Chromosome 8P: Insights from the TREND Community

Understanding Chromosome 8P: Insights from the TREND Community

In our third installment from our series of reports provided by our partner TREND Community, we are going to be focusing on a different condition over four weeks.  This week…

Continue Reading Understanding Chromosome 8P: Insights from the TREND Community
Reducing the Risk of Heart Attacks and Strokes with a Few Steps a Day

Reducing the Risk of Heart Attacks and Strokes with a Few Steps a Day

A new study recently published in the European journal of Preventive Cardiology and reported by Medical News Today, noted that individuals who added extra steps plus reasonable speed to their…

Continue Reading Reducing the Risk of Heart Attacks and Strokes with a Few Steps a Day
AbbVie’s IL-1 Drug Falters in Phase 2 Ulcerative Colitis Trial: What Happened and What’s Next?

AbbVie’s IL-1 Drug Falters in Phase 2 Ulcerative Colitis Trial: What Happened and What’s Next?

AbbVie, a global biopharmaceutical leader, has reported disappointing results from a phase 2 clinical trial evaluating its interleukin-1 (IL-1) targeting drug, ABBV-668, as a monotherapy for patients with moderate to…

Continue Reading AbbVie’s IL-1 Drug Falters in Phase 2 Ulcerative Colitis Trial: What Happened and What’s Next?
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You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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