• About
    • Meet Our Contributors
    • Meet Our Partners
    • Meet the Patient Worthy Team
    • Collaborative Content On Patient Worthy
  • Diseases
  • Share Your Story
    • Patient Worthy Content Submission Guidelines
    • Patient Worthy Writing Prompts
    • Submit Your Story
    • Patient Stories
  • Resources
    • Library
    • Events
    • Patient Worthy FAQs
  • Podcast
  • Contact
Menu
  • About
    • Meet Our Contributors
    • Meet Our Partners
    • Meet the Patient Worthy Team
    • Collaborative Content On Patient Worthy
  • Diseases
  • Share Your Story
    • Patient Worthy Content Submission Guidelines
    • Patient Worthy Writing Prompts
    • Submit Your Story
    • Patient Stories
  • Resources
    • Library
    • Events
    • Patient Worthy FAQs
  • Podcast
  • Contact
  • Join PW
Click Here To Share Your Story with Narcolepsy
Click Here to Read Real Stories From Patients And Caregivers
Click Here To Share Your Story With MASH

1527 Search Results Found

You searched for: "study of the week"
  1. Home>
  2. Search results for “study of the week”>
  3. Page 52
Racing Toward Relief: How One Biotech’s New Drug Targets a Genetic Skin Crisis

Racing Toward Relief: How One Biotech’s New Drug Targets a Genetic Skin Crisis

When life-threatening pustules suddenly erupt across the body accompanied by systemic inflammation, generalized pustular psoriasis (GPP) patients face a medical crisis with few treatment options. As reported by PharmaBiz.com, Vanda…

Continue Reading Racing Toward Relief: How One Biotech’s New Drug Targets a Genetic Skin Crisis
Eccogene Launches MOSAIC Trial to Test Dual Mechanisms Against Metabolic Liver Disease

Eccogene Launches MOSAIC Trial to Test Dual Mechanisms Against Metabolic Liver Disease

Eccogene, a clinical-stage biopharmaceutical company, has announced enrollment of the first patient in MOSAIC, a Phase 2a clinical trial investigating two novel oral small molecules for treating metabolic dysfunction-associated steatohepatitis…

Continue Reading Eccogene Launches MOSAIC Trial to Test Dual Mechanisms Against Metabolic Liver Disease
Breakthrough in COPD Management: GSK’s Nucala Advances Toward European Approval for Eosinophilic Patients

Breakthrough in COPD Management: GSK’s Nucala Advances Toward European Approval for Eosinophilic Patients

GSK announced a significant milestone in respiratory medicine as the European Medicines Agency's Committee for Medicinal Products for Human Use (CHMP) has recommended approval of Nucala (mepolizumab) for treating uncontrolled…

Continue Reading Breakthrough in COPD Management: GSK’s Nucala Advances Toward European Approval for Eosinophilic Patients
An Unexpected Liver Transplant Part 4 – The Journey to Disney World

An Unexpected Liver Transplant Part 4 – The Journey to Disney World

“We’re going to Disney World!” That's what all the winners say, right? When the big game is over and the team has won the championship, the winners say, for a…

Continue Reading An Unexpected Liver Transplant Part 4 – The Journey to Disney World
Universal-Target Vaccine Shows Early Promise in Rare Liver Cancer Affecting Youth

Universal-Target Vaccine Shows Early Promise in Rare Liver Cancer Affecting Youth

An experimental cancer vaccine from the Johns Hopkins Kimmel Cancer Center and the Bloomberg~Kimmel Institute for Cancer Immunotherapy has delivered encouraging results in a phase I trial for fibrolamellar carcinoma…

Continue Reading Universal-Target Vaccine Shows Early Promise in Rare Liver Cancer Affecting Youth
First-in-Human Gene Therapy Offers Hope for Hunter Syndrome: Oliver’s Remarkable Turnaround

First-in-Human Gene Therapy Offers Hope for Hunter Syndrome: Oliver’s Remarkable Turnaround

Three-year-old Oliver Chu has stunned clinicians after becoming the first person with Hunter syndrome (MPS II) to receive an experimental gene therapy and showing striking early gains. Hunter syndrome is…

Continue Reading First-in-Human Gene Therapy Offers Hope for Hunter Syndrome: Oliver’s Remarkable Turnaround
NHS Fast-Tracks Glofitamab, Expanding Curative Options for Aggressive Lymphoma

NHS Fast-Tracks Glofitamab, Expanding Curative Options for Aggressive Lymphoma

Hundreds more patients in England with relapsed or refractory diffuse large B-cell lymphoma (DLBCL) will gain earlier access to glofitamab (Columvi) after new guidance from the National Institute for Health…

Continue Reading NHS Fast-Tracks Glofitamab, Expanding Curative Options for Aggressive Lymphoma
FDA Approves Evaluating the OcoMate Dx Analysis System

FDA Approves Evaluating the OcoMate Dx Analysis System

The developer of the Promega OncoMate MSI Dx Analysis System recently announced the FDA’s approval of the system identifying patients who may benefit from the combination of Lenvatinib (Lenvima) and…

Continue Reading FDA Approves Evaluating the OcoMate Dx Analysis System
  • Go to the previous page
  • 1
  • …
  • 49
  • 50
  • 51
  • 52
  • 53
  • 54
  • 55
  • …
  • 191
  • Go to the next page
Finding Strength Together: Scott and Katie’s Journey with Advanced Kidney
You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
Read Full Story Here
We believe rare disease patients are people, not a diagnosis. Through education, awareness and some humor, we help patients, caregivers and support persons by providing relevant and often inspirational news and stories.
Our goals are to share stories, cultivate strong community, provide the latest medical findings, connect people and pioneer production of patient worthy information. Help us attain these goals by telling us a little bit about yourself!

Let’s Work Together!

Partner With Us
Submit a Story

Keep Up to Date

Subscribe to Our Newsletter
Check Out Rare Events
Get Inspired By Our Memes

Learn More

About Us
Rare Diseases and Conditions
Terms of Use
Privacy Notice
Privacy Policy for CA Residents
EU/UK Privacy Notice
Data Privacy Framework: Consumer Privacy Policy
Consumer Health Data Privacy Policy
Cookie Notice

Facebook-f Twitter Instagram Podcast Youtube Tiktok Linkedin-in Pinterest Envelope

© Copyright 2024 Patient Worthy

Sign Up With a Patient Worthy Account and Share Your Rare Story

- OR -

Sign Up For Our Patient Panel

Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.

More Info

We're Happy You're Here!

What best describes you when it comes to rare disease? (check all that apply)

What rare disease(s)/conditions are most important to you?

Visit Home Page or

Thank you for signing up for a Patient Worthy Account!

Have a rare disease story to share? Let us know

Share Story

- OR -

Sign Up For Our Patient Panel

Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.

More Info