Search Results for “study of the week” – Page 55

“Being Okay” – Kylie’s NF1 Journey

When we are faced with an obstacle, big or small, we supposedly pick one of two options: to fight it or to run away. Nowadays, they say there are more…

Alkermes’ Alixorexton Shows Promise in Narcolepsy Type 1: Vibrance-1 Phase 2 Results to Be Unveiled at World Sleep 2025

Alkermes is set to present detailed positive results from its Vibrance-1 Phase 2 study of alixorexton, a novel, once-daily oral orexin 2 receptor agonist, in patients with narcolepsy type 1…

Vincenzo’s Journey with Glanzmann Thrombasthenia

Editor's Note: Patient Worthy is proud to bring you this story from our friends at the Glanzmann Research Foundation. To see the article in its original format, please click here.…

My Diagnosis Didn’t Silence Me, It Lit a Fire

Editor's Note: Patient Worthy is proud to bring you this story-share, originally written by Gwen Pike, founder of the podcast Empowerment in Illness. When I was in my twenties, life was…

Opinion: Use of Basket Trials to Solve Sleep Problems in Patients with Rare Diseases

In our third installment from our series of reports provided by our partner TREND Community, we are bringing you several reports that analyze the effects of sleep disorders. This week…

Exercise and Colon Cancer: Can Exercise Reprogram Genes? And Help Colon Cancer Survivors?

A new study conducted at the Huntsman Cancer Institute in Utah suggests that exercise has a beneficial effect on the body, such as reprogramming, that alters the gene’s function, identity…

Breaking Ground: Palvella Therapeutics Completes Enrollment in Phase 2 TOIVA Trial for QTORIN™ Rapamycin in Cutaneous Venous Malformations

Palvella Therapeutics, Inc. has announced a key milestone in the development of therapies for rare genetic skin diseases: the completion of enrollment in its Phase 2 TOIVA trial of QTORIN™…

Diagnosis and management of sleep disorders in Prader-Willi syndrome