• About
    • Meet Our Contributors
    • Meet Our Partners
    • Meet the Patient Worthy Team
    • Collaborative Content On Patient Worthy
  • Diseases
  • Share Your Story
    • Patient Worthy Content Submission Guidelines
    • Patient Worthy Writing Prompts
    • Submit Your Story
    • Patient Stories
  • Resources
    • Library
    • Events
    • Patient Worthy FAQs
  • Podcast
  • Contact
Menu
  • About
    • Meet Our Contributors
    • Meet Our Partners
    • Meet the Patient Worthy Team
    • Collaborative Content On Patient Worthy
  • Diseases
  • Share Your Story
    • Patient Worthy Content Submission Guidelines
    • Patient Worthy Writing Prompts
    • Submit Your Story
    • Patient Stories
  • Resources
    • Library
    • Events
    • Patient Worthy FAQs
  • Podcast
  • Contact
  • Join PW
Click Here To Share Your Story with Breast Cancer
Stay Tuned!
Click Here to Read Real Patient & Caregiver Stories

1614 Search Results Found

You searched for: "study of the week"
  1. Home>
  2. Search results for “study of the week”>
  3. Page 54
Ascletis Advances Obesity Pipeline With Two FDA IND Filings for Long-Acting Injectable Candidates

Ascletis Advances Obesity Pipeline With Two FDA IND Filings for Long-Acting Injectable Candidates

As reported on PharmaBiz, Ascletis Pharma has announced the submission of two Investigational New Drug (IND) applications to the US Food and Drug Administration (FDA) for experimental obesity treatments designed…

Continue Reading Ascletis Advances Obesity Pipeline With Two FDA IND Filings for Long-Acting Injectable Candidates
European Commission Expands Approval of Novartis Gene Therapy for Broader SMA Population

European Commission Expands Approval of Novartis Gene Therapy for Broader SMA Population

As reported on Pharmaceutical Technology, the European Commission has approved Novartis’ gene replacement therapy Itvisma (onasemnogene abeparvovec) for the treatment of children aged two years and older, adolescents, and adults…

Continue Reading European Commission Expands Approval of Novartis Gene Therapy for Broader SMA Population
Sonelokimab Shows Sustained One-Year Benefits in Hidradenitis Suppurativa, With Encouraging Early Results in Adolescents

Sonelokimab Shows Sustained One-Year Benefits in Hidradenitis Suppurativa, With Encouraging Early Results in Adolescents

As reported on Healio, new phase 3 data suggest that sonelokimab may offer durable disease control for patients with moderate to severe hidradenitis suppurativa (HS), with more than two-thirds of…

Continue Reading Sonelokimab Shows Sustained One-Year Benefits in Hidradenitis Suppurativa, With Encouraging Early Results in Adolescents
FDA Approved Therapy for Rare and Severe Kidney Disease for Children Twelve or Older

FDA Approved Therapy for Rare and Severe Kidney Disease for Children Twelve or Older

In recent reports on MSN and AdventLS, it was shared that, as a result of the pioneering efforts of Dr. Carla Nester and researchers at the Children’s Hospital of Iowa…

Continue Reading FDA Approved Therapy for Rare and Severe Kidney Disease for Children Twelve or Older
Grifols Starts Phase 3 Trial for a New, More Convenient Alpha-1 Treatment

Grifols Starts Phase 3 Trial for a New, More Convenient Alpha-1 Treatment

What Happened? The healthcare company Grifols announced in a recent press release that it has enrolled and dosed the very first patient in a new Phase 3 clinical trial called…

Continue Reading Grifols Starts Phase 3 Trial for a New, More Convenient Alpha-1 Treatment
FDA Extends Review of Praxis Epilepsy Drug Candidate Relutrigine by Three Months

FDA Extends Review of Praxis Epilepsy Drug Candidate Relutrigine by Three Months

As reported on BioSpace, Praxis Precision Medicines has received a three-month extension to the U.S. Food and Drug Administration’s review of relutrigine, its investigational therapy for rare genetic forms of…

Continue Reading FDA Extends Review of Praxis Epilepsy Drug Candidate Relutrigine by Three Months
FDA Expands Risankizumab Approval to Pediatric Patients With Plaque Psoriasis and Psoriatic Arthritis

FDA Expands Risankizumab Approval to Pediatric Patients With Plaque Psoriasis and Psoriatic Arthritis

As reported on Becker's Hospital Review, the FDA has approved risankizumab (Skyrizi) for use in children and adolescents aged 6 years and older with moderate-to-severe plaque psoriasis who are appropriate…

Continue Reading FDA Expands Risankizumab Approval to Pediatric Patients With Plaque Psoriasis and Psoriatic Arthritis
FDA Expands Approval of Roflumilast Cream (Zoryve) to Younger Children with Plaque Psoriasis

FDA Expands Approval of Roflumilast Cream (Zoryve) to Younger Children with Plaque Psoriasis

As reported on Healio, the U.S. Food and Drug Administration has broadened the indication for roflumilast cream 0.3% (Zoryve, Arcutis), allowing its use in children with plaque psoriasis as young…

Continue Reading FDA Expands Approval of Roflumilast Cream (Zoryve) to Younger Children with Plaque Psoriasis
  • Go to the previous page
  • 1
  • …
  • 51
  • 52
  • 53
  • 54
  • 55
  • 56
  • 57
  • …
  • 202
  • Go to the next page
The Mentor She Wished She Had - How Elizabeth Became a Lifeline for EB
Finding Strength Together: Scott and Katie’s Journey with Advanced Kidney
You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
We believe rare disease patients are people, not a diagnosis. Through education, awareness and some humor, we help patients, caregivers and support persons by providing relevant and often inspirational news and stories.
Our goals are to share stories, cultivate strong community, provide the latest medical findings, connect people and pioneer production of patient worthy information. Help us attain these goals by telling us a little bit about yourself!

Let’s Work Together!

Partner With Us
Submit a Story

Keep Up to Date

Subscribe to Our Newsletter
Check Out Rare Events
Get Inspired By Our Memes

Learn More

About Us
Rare Diseases and Conditions
Terms of Use
Privacy Notice
Privacy Policy for CA Residents
EU/UK Privacy Notice
Data Privacy Framework: Consumer Privacy Policy
Consumer Health Data Privacy Policy
Cookie Notice

Facebook-f Twitter Instagram Podcast Youtube Tiktok Linkedin-in Pinterest Envelope

© Copyright 2024 Patient Worthy

Sign Up With a Patient Worthy Account and Share Your Rare Story

- OR -

Sign Up For Our Patient Panel

Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.

More Info

We're Happy You're Here!

What best describes you when it comes to rare disease? (check all that apply)

What rare disease(s)/conditions are most important to you?

Visit Home Page or

Thank you for signing up for a Patient Worthy Account!

Have a rare disease story to share? Let us know

Share Story

- OR -

Sign Up For Our Patient Panel

Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.

More Info