AVR-RD-02 – Patient Worthy

AVR-RD-02 Earns Rare Pediatric Disease Designation for Gaucher Disease

Post author:Jessica Lynn
Post published:November 10, 2022
Post category:Gaucher Disease

The FDA created the Rare Pediatric Disease Designation and Priority Review Voucher Program to stimulate the development of therapies intended to treat, diagnose, or prevent rare pediatric diseases. These are…

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