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beta thalassemia major

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Shelby’s Gene Therapy Journey for Beta Thalassemia
source: shutterstock.com

Shelby’s Gene Therapy Journey for Beta Thalassemia

  • Post author:Rose Duesterwald
  • Post published:January 30, 2024
  • Post category:Beta Thalassemia/Beta Thalassemia Major/Beta thalassemia major

The agency in Guangzhou, China, that arranged three-year-old Shelby’s adoption by a family in the US disclosed to Michelle and Adam Campbell that Shelby had beta thalassemia disorder. Yet, that…

Continue Reading Shelby’s Gene Therapy Journey for Beta Thalassemia
Rare Classroom: Beta Thalassemia
source: shutterstock

Rare Classroom: Beta Thalassemia

  • Post author:James Moore
  • Post published:August 12, 2022
  • Post category:Beta Thalassemia/Beta Thalassemia Major/Beta thalassemia major

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…

Continue Reading Rare Classroom: Beta Thalassemia
Beta Thalassemia Major: This Couple Had a Baby to Save Their Son
source: pixabay.com

Beta Thalassemia Major: This Couple Had a Baby to Save Their Son

  • Post author:James Moore
  • Post published:October 23, 2020
  • Post category:Beta Thalassemia/Beta Thalassemia Major/Rare Disease

According to a story from Vice World News, the Solanki family, who are residents of Ahmedabad, the largest city in India's western state of Gujarat, recently took action to save…

Continue Reading Beta Thalassemia Major: This Couple Had a Baby to Save Their Son
FDA Approves New Treatment for Anemia in Beta Thalassemia Patients
source: pixabay.com

FDA Approves New Treatment for Anemia in Beta Thalassemia Patients

  • Post author:James Moore
  • Post published:November 22, 2019
  • Post category:Beta Thalassemia/Beta thalassemia major/Timely

A press release from the US Food and Drug Administration (FDA) is announcing the approval of a new treatment for anemia in adult patients with the rare blood disorder beta…

Continue Reading FDA Approves New Treatment for Anemia in Beta Thalassemia Patients
Major Gene Therapy Progress for β-thalassemia Major
https://pixabay.com/en/fireworks-celebration-bright-pink-1759/

Major Gene Therapy Progress for β-thalassemia Major

  • Post author:Trudy Horsting
  • Post published:July 12, 2017
  • Post category:Beta Thalassemia Major/Rare Disease

β-thalassemia major is a rare blood condition that necessitates a lifetime of blood transfusions. Despite advancements in treatments, the perfect cure has yet to be found. Bluebird Bio, Inc. is…

Continue Reading Major Gene Therapy Progress for β-thalassemia Major
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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