CDLK5 deficiency disorder Archives

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A Possible Treatment for CDKL5 Deficiency Disorder has Earned Rare Pediatric Disease Designation

Post author:James Moore
Post published:August 11, 2020
Post category:CDKL5 Status epilepticus Tuberous Sclerosis

According to a story from BioSpace, the pharmaceutical company Marinus Pharmaceuticals, Inc. announced recently that its investigational product candidate ganaxolone has earned Rare Pediatric Disease designation from the US Food…

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A Possible Treatment for CDKL5 Deficiency Disorder has Earned Rare Pediatric Disease Designation

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