Galafold

EC Approves Galafold for Adolescent Fabry Disease with an Amenable Mutation
Source: https://unsplash.com/photos/ZHys6xN7sUE

EC Approves Galafold for Adolescent Fabry Disease with an Amenable Mutation

On August 2, 2021, biotechnology company Amicus Therapeutics ("Amicus") shared that its oral treatment Galafold (migalastat) was approved by the European Commission (EC) for the treatment of adolescent patients (ages…

Continue Reading EC Approves Galafold for Adolescent Fabry Disease with an Amenable Mutation
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