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Luxturna

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Doctors Use Luxturna to Restore Vision in 6-Year-Old with RP
source: pixabay.com

Doctors Use Luxturna to Restore Vision in 6-Year-Old with RP

  • Post author:Jessica Lynn
  • Post published:August 30, 2023
  • Post category:Retinitis pigmentosa

Galila Yohannes’ parents, who originally hail from Eritrea, brought their family to Israel for a better life. And while they never would have expected what came next, this move likely…

Continue Reading Doctors Use Luxturna to Restore Vision in 6-Year-Old with RP
Gene Therapy Luxturna Will Cost $850,000 To Patients With Rare Eye Disease
Source: Pixabay

Gene Therapy Luxturna Will Cost $850,000 To Patients With Rare Eye Disease

  • Post author:Meagan Fulps
  • Post published:January 8, 2018
  • Post category:Rare Disease/RPE65-associated Leber Congenital Amaurosis

The FDA passed along their nod of approval for the sought after gene therapy treatment, Luxturna, reported Engadget. This will be used to help aid those made blind by a…

Continue Reading Gene Therapy Luxturna Will Cost $850,000 To Patients With Rare Eye Disease
Luxturna Gene Therapy Could Change the Game in Treating Inherited Blindness
Skitterphoto / Pixabay

Luxturna Gene Therapy Could Change the Game in Treating Inherited Blindness

  • Post author:Octavia Walker
  • Post published:December 19, 2017
  • Post category:Rare Disease/RPE65-associated Leber Congenital Amaurosis

On this season of America's Got Talent, the world met Christian Guardino. I was one of millions who heard his beautiful singing voice as he belted out his song onstage.…

Continue Reading Luxturna Gene Therapy Could Change the Game in Treating Inherited Blindness
This Family Has High Hopes for Gene Therapy Approval
Source: Pixabay

This Family Has High Hopes for Gene Therapy Approval

  • Post author:Andres Rovira
  • Post published:November 15, 2017
  • Post category:RPE65-associated Leber Congenital Amaurosis

Sam and Anna Beiler have not one, but two children with a rare degenerative disease that causes blindness. As of now, there is no treatment. Last month, however, the FDA…

Continue Reading This Family Has High Hopes for Gene Therapy Approval
Our First $1M Drug! Who’s Buying?
Source: Pixabay

Our First $1M Drug! Who’s Buying?

  • Post author:Andres Rovira
  • Post published:October 18, 2017
  • Post category:Rare Disease

As the world turns, so do advancements in gene therapy. Technology is changing our world so drastically that soon gene therapy will be simplified into a one-shot treatment. With it,…

Continue Reading Our First $1M Drug! Who’s Buying?
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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