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mucopolysaccharidosis II (MPS II)

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Study: Idursulfase Therapy is a Safe Treatment for Hunter Syndrome (MPS II)
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Study: Idursulfase Therapy is a Safe Treatment for Hunter Syndrome (MPS II)

  • Post author:Kendall Mason
  • Post published:December 5, 2019
  • Post category:MPS II/MPS II (Hunter Syndrome)/Mucopolysaccharidosis

  A recent meta-analyses of clinical studies and case reports that examined the safety of idursulfase therapy, which is an enzyme therapy, has shown that this form of treatment is…

Continue Reading Study: Idursulfase Therapy is a Safe Treatment for Hunter Syndrome (MPS II)
Sangamo Updates on Beta Thalassemia, MPS, and Hemophilia Trials

Sangamo Updates on Beta Thalassemia, MPS, and Hemophilia Trials

  • Post author:Scott Carlson
  • Post published:June 17, 2019
  • Post category:Beta Thalassemia/Hemophilia A/MPS II

According to a publication from Fierce Biotech, Biotech company Sangamo recently updated investors on three trials it has underway testing experimental forms of gene and cell therapies. The trials are…

Continue Reading Sangamo Updates on Beta Thalassemia, MPS, and Hemophilia Trials
Hunter Syndrome Taking Less and Less Lives Prematurely
Source: www.pixabay.com

Hunter Syndrome Taking Less and Less Lives Prematurely

  • Post author:Erica Zahn
  • Post published:March 22, 2017
  • Post category:MPS II (Hunter Syndrome)/Rare Disease

To walk in the shoes of others is sometimes what it takes to truly understand their journey. So when I came across the blog, Jason and Justin's Journey x2 - Don't Stop…

Continue Reading Hunter Syndrome Taking Less and Less Lives Prematurely
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
*cancer that cannot be removed with surgery or has spread to other parts of the body. GEJ= gastroesophageal junction (where the esophagus joins the stomach)
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