Experimental Gene Therapy Program for Hunter Syndrome (MPS II) Begins Expanding
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Experimental Gene Therapy Program for Hunter Syndrome (MPS II) Begins Expanding

According to a story from PR Newswire, the biotechnology company REGENXBIO Inc. has recently announced plans to expand its RGX-121 developmental program. RGX-121 is being developed as a potential one-time…

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Study: Idursulfase Therapy is a Safe Treatment for Hunter Syndrome (MPS II)
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Study: Idursulfase Therapy is a Safe Treatment for Hunter Syndrome (MPS II)

  A recent meta-analyses of clinical studies and case reports that examined the safety of idursulfase therapy, which is an enzyme therapy, has shown that this form of treatment is…

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Company Seeks to Treat Hunter Syndrome (MPS II) in China With New Drug Application
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Company Seeks to Treat Hunter Syndrome (MPS II) in China With New Drug Application

According to a story from BioSpace, the biopharmaceutical company CANBridge Pharmaceuticals announced that it has recently submitted a New Drug Application with China's National Medicinal Products Administration (NMPA) for its…

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Experimental Treatment for Hunter Syndrome Earns Rare Pediatric Disease Designation and Orphan Drug Designation
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Experimental Treatment for Hunter Syndrome Earns Rare Pediatric Disease Designation and Orphan Drug Designation

According to a story from globenewswire.com, the biopharmaceutical company Denali Therapeutics, Inc. has recently announced that its experimental product candidate DNL310, which is currently being developed as a treatment for…

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This Just In: India Never Implemented their Rare Disease Policy as Promised
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This Just In: India Never Implemented their Rare Disease Policy as Promised

We all got really excited last year when India implemented a new plan to benefit rare disease patients. It was called the National Rare Disease Policy. Basically, it put 12.86…

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A Mother’s Fundraising Campaign Could be Critical For Finding a Cure For Hunter Syndrome
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A Mother’s Fundraising Campaign Could be Critical For Finding a Cure For Hunter Syndrome

According to a story from The Tennessean, mother Melissa Hogan has been inspired by her son Case's Hunter syndrome to start a nonprofit organization called Project Alive. The primary purpose…

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