PTC-AADC – Patient Worthy

PTC-AADC Shows Benefits for Patients with AADC Deficiency, Data Shows

Post author:Jessica Lynn
Post published:October 5, 2021
Post category:Aromatic amino acid decarboxylase deficiency

Recently, biopharmaceutical company PTC Therapeutics, Inc. performed a five-year data analysis to evaluate the continued safety, efficacy, and tolerability of PTC-AADC. The company developed this novel gene therapy to improve…

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