RPE65-mediated inherited retinal dystrophy

Luxturna Gene Therapy Could Change the Game in Treating Inherited Blindness

Post author:Octavia Walker
Post published:December 19, 2017
Post category:Rare Disease RPE65-associated Leber Congenital Amaurosis

On this season of America's Got Talent, the world met Christian Guardino. I was one of millions who heard his beautiful singing voice as he belted out his song onstage.…

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