Gene Therapy Made Simple, Just for You

At PatientWorthy, we’ve talked a lot about gene therapy, but we’ve never really taken the time to explain it. What the heck is gene therapy? How does it work?

Well, like your relationship with pharmaceutical companies, it’s complicated. So, let’s aim for simplicity.

Gene therapy, according to Genetic Literacy Project, is when a patient’s stem cells are surgically removed, altered and combined with corrected versions of the original defective gene, and then, essentially, put back into the patient. Easy, enough.

Don’t confuse gene therapy with stem-cell transplants–they are very different, the latter involving a donor and a host.

In recent years, a lot of research has gone into gene therapy, for conditions like beta-thalassemia, primary immune deficiency diseases such as  severe combined immunodeficiency (SCID), and Wiskott-Aldrich syndrome.

Thanks to gene therapy, people with chronic disease can look to their futures a bit more hopeful.

neil degrasse tyson mind blown
Science is a mind-blowing endeavor!

And there you have it. Gene therapy in a nut-shell. Now you can impress all your friends at parties with your new-found knowledge.

Read more about gene therapy here.

Lady Kehveen Abernathy

Lady Kehveen Abernathy

Lady Kehveen Abernathy, of noble birth (or so she’d like to believe), is what many would call a youthful “old soul.” As a self-proclaimed “caregiver to the world,” impassioned about life, triumph, and all things beauty, Lady Kehveen strives to love others, seek understanding, and most importantly, spread awareness. But don’t let her sweet demeanor deceive you. Dressed to the nines over corset and petticoat, she’s made it her mission to defend the innocent and fight all things evil on this Earth. And being no stranger to chronic disease, she knows exactly where to start.

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