Editor’s Choice: Treatments, Methods and Strategies in Coping with Rare Diseases

Happy August Patient Worthy Peeps!

This week, we have some awesome posts to keep you up-to-date on some of the latest rare disease developments.

There’s news on a hopeful possible treatment for ALD, cystic fibrosis treatment from Vertex, a new way to measure Parkinson’s progression and strategies for dealing with PD.

So sit back and enjoy this week’s Editor’s Choice.


A Possible Treatment for the Rarest of Adrenoleukodystrophy

ALD is a super rare disease with debilitating symptoms.

Read about a possible treatment for the rarest form here!


Vertex Pharmaceuticals on the Verge of a New, More Effective Cystic Fibrosis Treatment

Cystic fibrosis has come a long way in the past 50 years.

Could this new treatment be the next step toward a cure?


A New Method to Measure Parkinson’s Disease Progression

Parkinson’s is a devastating, progressive disease.

Read here on a new way to track it.


Top Strategies for Helping Loved Ones with Parkinson’s Dementia

Dementia in any form is incredibly difficult for the patient and family.

Read here on tips for how to deal with it.


Do you have a rare disease experience of your own? Share with us here.

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