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Daily Archives: September 8, 2025

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No Time to Wait: NC Families and Researchers Urge Faster FDA Action on Rare Disease Drugs

No Time to Wait: NC Families and Researchers Urge Faster FDA Action on Rare Disease Drugs

  • Post author:Bree Clare
  • Post published:September 8, 2025
  • Post category:Barth Syndrome

Families and researchers in North Carolina are making urgent appeals to the FDA, highlighting the desperate need for faster approval of drugs for rare and ultra-rare diseases that threaten children’s…

Continue Reading No Time to Wait: NC Families and Researchers Urge Faster FDA Action on Rare Disease Drugs
Is Your Cancer Really Gone? 5 Things You Need to Know About Molecular Residual Disease (MRD) Tests

Is Your Cancer Really Gone? 5 Things You Need to Know About Molecular Residual Disease (MRD) Tests

  • Post author:PW Collaborator
  • Post published:September 8, 2025
  • Post category:Rare Disease

After cancer treatment, many patients are left with a haunting uncertainty: Is it really gone—and will it stay that way? Even when scans appear clear, questions linger. Now, a newer…

Continue Reading Is Your Cancer Really Gone? 5 Things You Need to Know About Molecular Residual Disease (MRD) Tests
Verzenio Extends Survival in Early Breast Cancer, Says Lilly’s Latest Study

Verzenio Extends Survival in Early Breast Cancer, Says Lilly’s Latest Study

  • Post author:Bree Clare
  • Post published:September 8, 2025
  • Post category:Breast Cancer

Eli Lilly’s breast cancer drug Verzenio (abemaciclib) has achieved a significant milestone, with new study results showing it helps people with a common form of early-stage breast cancer live longer.…

Continue Reading Verzenio Extends Survival in Early Breast Cancer, Says Lilly’s Latest Study
The Mentor She Wished She Had - How Elizabeth Became a Lifeline for EB
Finding Strength Together: Scott and Katie’s Journey with Advanced Kidney
You Are Not Alone: Empowering the Advanced Kidney Cancer Community
Finding Light Through Story-The Power of Ambassadorship in the Endometrial Cancer Community
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