As reported on PR Newswire, the US Food and Drug Administration has granted Breakthrough Therapy designation to Kowa’s investigational therapy K-808 (pemafibrate) for primary biliary
As reported on The ASCO Post, perioperative treatment with enfortumab vedotin-ejfv plus pembrolizumab resulted in superior event-free survival, overall survival, and pathologic response rates compared
As reported by the BBC, the Ebola outbreak in DR Congo was declared in May 2026 and is now the second worst on record with
Editor’s Note: The following article was originally written by Dr. Linda Bluestein. Linda Bluestein, MD, is a board-certified anesthesiologist and internationally recognized expert in hypermobility
As reported on Gizmodo, Samsung has announced that its Galaxy Ring will soon support an FDA-cleared sleep apnea risk detection feature, making it the first
Editor’s Note: The following patient story was submitted to us by Christoph Muth, a 52-year-old German man currently residing in Thailand. I am living with
As reported by The Manila Times, Axsome Therapeutics has announced the initiation of its Phase 3 CLARITY clinical trial evaluating solriamfetol as a potential treatment
According to a press release from Texas A &M, researchers are using artificial intelligence to narrow drug choices and make shared data easier to use. Tuberculosis drug
A team from Minnesota University has created a synthetic cell that includes lifeless chemicals and created a synthetic cell that will grow, reproduce, and even
Editor’s Note: Patient Worthy is honored to share this article from our friends at Elephants & Tea, originally written by Kiki Khan, a leukemia survivor.
Editor’s Note: This post was written and submitted to us by Jon Scheinman, and originally shared on LinkedIn. To see the article in its original
As reported on Drugs, Eli Lilly has reported positive topline findings from two additional Phase 3 trials of retatrutide, its investigational triple hormone receptor agonist
As reported on PharmaBiz, AstraZeneca has reached an important regulatory milestone in Europe after the European Medicines Agency’s Committee for Medicinal Products for Human Use
As reported on PharmaBiz, the European Medicines Agency’s Committee for Medicinal Products for Human Use (CHMP) has issued a positive recommendation supporting approval of AstraZeneca
As reported on Fierce BioTech, Roche has discontinued development of its investigational T-cell engager (TCE) RG6382 for systemic lupus erythematosus (SLE), following an internal review
Researchers from La Jolla Institute for Immunology (LJI), Scripps Research, and IAVI have reported a major advance in HIV vaccine development, demonstrating an experimental vaccine
Coats disease, is a rare retina condition diagnosed primarily in children. Symptoms may include, eye drift, blurry vision, the appearance of a white or silver
As reported on Stock Titan, the European Medicines Agency’s Committee for Medicinal Products for Human Use (CHMP) has issued a positive opinion recommending approval of
hATTRNextGen Do you know your risk for hereditary amyloidosis ?
This content isn't available right now
When this happens, it's usually because the owner only shared it with a small group of people, changed who can see it or it's been deleted.
Fabry Support & Information GroupIndividuals and families affected by Fabry disease are invited to join FSIG at WORLDFair 2026 on September 18 at the University of Minnesota Landscape Arboretum in Chaska, Minnesota. This free educational event led by the Genetics Department of University of Minnesota Twin Cities, offers an opportunity to connect with experts, learn about the latest developments in Fabry disease research and care, and meet others who understand the rare disease journey. Whether you attend in person or via Zoom, you'll gain valuable information, encouragement, and community. Reserve your spot today. REGISTER at worldfair.health.
We look forward to seeing you!
#FSIG30 #PatientEducation #FabryDisease #RareDisease #EmpoweringPatients #Research #LysosomalStorageDiseases
www.facebook.com
Advancing the prevention, early diagnosis and successful treatment of life-threatening blood clots. Together we can Stop the Clot®.
© Copyright 2024 Patient Worthy
Sign Up With a Patient Worthy Account and Share Your Rare Story
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
- OR -
Make a difference, share your experiences and get paid. Opt-in and join Patient Worthy's panel for paid opportunities such as surveys, market research, patient advisory panels and more.
