Remix Therapeutics has achieved a significant regulatory milestone with the U.S. Food and Drug Administration granting Fast Track designation to REM-422, a first-in-class small molecule
My whole life growing up, there was this specific buzzing sound that would come alive on the sunniest of days. I’ve been told over the
On 12/12/2025, I was admitted into the ER for a thrombectomy due to a bilateral pulmonary embolism. While I am overweight and sometimes eat like
The American Nutrition Association (ANA) has announced a collaborative initiative with Jazz Pharmaceuticals designed to advance evidence-based nutritional education for individuals living with narcolepsy and
This patient story is sponsored by Chiesi Global Rare Diseases and is promoted through the Patient Worthy Collaborative Content program. We only publish content that
Patients living with chronic or rare diseases and the caregivers coordinating appointments, medications, and daily life often carry a quiet question alongside the medical work:
The Dravet Syndrome Foundation of Spain hosted its 2026 Annual Family Meeting on March 20 at the Rafaela Ybarra School in Madrid, bringing together roughly 100
The pharmaceutical industry celebrates a significant victory for rare disease patients as the Food and Drug Administration approved Denali Therapeutics’ groundbreaking enzyme replacement therapy for
As reported on PharmaBiz, the US Food and Drug Administration (FDA) has approved Novo Nordisk’s higher‑dose formulation of semaglutide, Wegovy HD (7.2 mg once weekly),
I used to be really active: swimming, Tai Chi every week, practicing yoga. So, when I first felt persistent rib and back pain in late
GSK has announced a significant advancement in liver disease treatment with FDA approval of Lynavoy (linerixibat), marking the first medication specifically approved in the United
My diagnosis of rheumatic heart disease came on suddenly. I remember being 12, sitting at the doctor’s office, and was told that I have a
Researchers at Florida Atlantic University (FAU) have identified a cellular pathway that allows brain cells to share proteins and other toxic material. The study was
Lupin, a globally recognized pharmaceutical company, has achieved a significant regulatory milestone with the receipt of tentative FDA approval for Pitolisant tablets in strengths of
Editor’s Note: Patient Worthy is honored to present this article, shared with us by our friends at the Steatotic Liver Foundation (formerly the Fatty Liver
Fight. I don’t think that those who aren’t in the Huntington’s Disease community understand what the word FIGHT truly means to those of us inside
My name is Amanda. I was diagnosed with a genetic connective tissue disease called Hypermobile Ehlers-Danlos Syndrome (h-EDS) about four years ago. However, the diagnosis
My name is Faye. I’m blessed to be the wife of the love of my life, Brad, and the proud mom of two extraordinary boys
April 5th is Barth Syndrome Awareness Day - a time to shine a light on a rare genetic condition that affects the heart, muscles, and immune system. Barth Syndrome may be a little known, but for those living with it, the challenges are very real. Raising Awareness helps drive research, early diagnosis, and support for families who need it most.
Every voice matters. By learning, sharing, and advocating, we can help create a future where rare diseases like this are better understood and treated. #barthsyndromeawareness #geneticdisorders #PatientWorthy
Head and neck cancers affect vital parts of how we speak, breathe, and connect with the world- yet many people don't recognize the early warning signs. Persistent sore throat, difficulty swallowing, voice change, or unusual lumps should never be ignored. Early detection can save lives.
Awareness isn't just knowledge- it's action. Protect your health by avoiding tobacco, limiting alcohol, considering HPV vaccination, and seeking medical advice when something feels off. Your voice matters- take care of it.
#headandneckcancer #preventcancer #PatientWorthy
April is IBS Awareness Month 💜
Irritable Bowel Syndrome affects millions, yet so many suffer in silence. IBS is real, complex, and deserving of understanding—not dismissal. Let’s break the stigma, share knowledge, and support those living with chronic digestive conditions every day.
#IBSAwarenessMonth #GutHealth #ChronicIllnessAwareness #PatientWorthy
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