Colorectal cancer
Raspberry Sorbet Swirls in the Sky
Editor’s Note: This poem, originally written by Spence Shishido, was shared with Patient Worthy by our friends at Elephants & Tea. To see the poem
Deucrictibant Provides Rapid Relief for Hereditary Angioedema Attack Symptoms
Incyte Reports Positive Phase III Results for Tafasitamab in First-Line DLBCL Treatment
Repurposing Breast Cancer Drug Offers New Hope for Acute Myeloid Leukemia Patients
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Rare Disease
Hereditary Fructose Intolerance (HFI) UK – an HFI Support Charity
This charity has been set up to offer research based and lived experience, advice and support. Aims: To support any individual of any age with
Metabolic dysfunction-associated steatohepatitis
FDA Approves First AI Tool to Advance MASH Drug Development
As reported by Healio, the U.S. Food and Drug Administration (FDA) has officially qualified AIM-MASH AI Assist, marking a milestone as the first artificial intelligence
Kawasaki syndrome
From Plasma Recipient to Empowered Donor: Oliver’s Full Circle Journey
Sixteen years ago, Nate Appleman, a celebrated chef, faced every parent’s worst nightmare when his two-year-old son, Oliver, fell ill. Oliver’s diagnosis was a complete
Rare Disease
Her Life Changed at a Red Light. Life and Love with HIV is Possible.
My name is Jessica Glaspie, and I have been living with HIV for over 15 years! A lot of people think that life and love
Chronic obstructive pulmonary disease (COPD)
Breakthrough in COPD Management: GSK’s Nucala Advances Toward European Approval for Eosinophilic Patients
GSK announced a significant milestone in respiratory medicine as the European Medicines Agency’s Committee for Medicinal Products for Human Use (CHMP) has recommended approval of
ADHD
FDA Approves LumosityRx as Prescription Digital Therapeutic for Adult ADHD
Lumos Labs has received FDA 510(k) approval for LumosityRx, a prescription version of its well-known Lumosity brain training platform. As reported by Fierce BioTech, The
Rare Disease
An Unexpected Liver Transplant Part 4 – The Journey to Disney World
“We’re going to Disney World!” That’s what all the winners say, right? When the big game is over and the team has won the championship,
Cancer
Eli Lilly’s Jaypirca Positions Itself as Superior Alternative to Imbruvica in Blood Cancer Treatment
Eli Lilly presented compelling clinical evidence positioning its BTK inhibitor Jaypirca as a potentially superior treatment option compared to the established blood cancer therapy Imbruvica,
Rare Disease
FDA Unveils TEMPO Pilot to Advance Digital Health for Chronic Disease Care
In a recent statement, The U.S. Food and Drug Administration (FDA) has introduced the Technology-Enabled Meaningful Patient Outcomes (TEMPO) Pilot, a groundbreaking initiative aimed at
Wiskott-Aldrich Syndrome
FDA Officially Green-Lights First Gene Therapy for Wiskott-Aldrich Syndrome
In a statement by the FDA, the U.S. Food and Drug Administration has authorized Waskyra (etuvetidigene autotemcel), the first gene therapy designed to treat Wiskott-Aldrich
Duchenne Muscular Dystrophy
Biotech Innovation Accelerates: Four Companies Show Promising Pipeline Progress
The biotech sector witnessed significant momentum as four clinical-stage companies announced compelling data across muscular dystrophy, immunology, and obesity treatment areas, triggering substantial stock market
Rare Disease
Human Gut Cells Reveal Unexpected Role in Celiac Disease
As reported by MedicalXpress, Researchers have uncovered a surprising immune function in specialized intestinal cells that may reshape our understanding of gut health and autoimmune
Breast Cancer
Giredestrant Emerges as Breakthrough Adjuvant Therapy for Early-Stage ER-Positive Breast Cancer
Genentech announced landmark clinical trial results demonstrating that giredestrant, an investigational selective estrogen receptor degrader (SERD), significantly outperforms standard endocrine therapy in treating early-stage ER-positive
Dravet Syndrome
Patient Worthy Congratulates the Dravet Syndrome Foundation of Spain
Madrid, December 3, 2025 – The research laboratory of the Dravet Syndrome Foundation was one of the initiatives awarded 3,000 Euros in the 11th edition
C3 Glomerulopathy
The FDA Approves a Drug that Brought a 67% Reduction in a Life-Threatening Kidney Disease Affecting Young Adults and Children
A rare and life-threatening kidney disease affecting young adults and children finally has an effective and approved therapy due to the pioneering and leadership of
Rare Disease
NYU Langone Doctors Transplanted a Pig Kidney into a Brain Dead Patient Reversing Rejection Twice
A team of doctors at NYU Langone transplanted a pig kidney into a brain-dead patient and reversed its rejection twice during the 61-day study. Currently,
Multiple Myeloma
Early Use of Tecvayli Shows Potential for Functional Cure in Multiple Myeloma
As reported on BioPharmaDive, new clinical trial data presented at the American Society of Hematology (ASH) annual meeting suggests that an early treatment regimen combining
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The FDA has granted full approval to Rubraca (rucaparib) for the treatment of BRCA-Mutated metastatic castration-resistant prostate cancer (mCRPC). Read more here:
patientworthy.com/2026/01/07/fda-grants-full-approval-to-rucaparib-for-brca-mutated-mcrpc/
Patient Worthy is looking for individuals who are interested in sharing their experiences with Diffuse Large B-Cell Lymphoma (DLBCL). Be the reason someone feels seen, supported, and inspired! If you're interested in learning more or joining the conversation this week, visit patientworthy.com for the latest information. If you have a story to share, click here: bit.ly/4dV7gru #DLBCL #shareyourstory #PatientWorthy
Insights Wanted: HER2+ mBC
