Anna is from England and recently finished her undergraduate degree. She has an interest in medicine and enjoys writing. In her spare time she likes to cook, hike, and hang out with cats.
Kruz and his sister Paizlee are the only known siblings diagnosed with the ultra-rare condition Schimke Immuno-Osseous Dysplasia. Their parents, Jessica and Kyle, are doing everything they can to raise…
The US Food and Drug Administration has awarded Orphan Drug Designation to the drug lenabasum as a treatment for dermatomyositis. The use of lenabasum for treating this condition, and others,…
The organisations Takeda Pharmaceutical Company and Ovid Therapeutics are collaborating over the development of the experimental drug TAK-935/OV935 as a possible treatment for several rare epilepsy syndromes. Takeda has just…
Results from a Phase 2 clinical trial comparing the effects of baricitinib to a placebo in patients with systemic lupus erythematosus (SLE) have been announced. For more detailed information, please…
Researchers from the Newcastle University are investigating the personal and financial impacts of persistent facial pain on patients in the UK, and what can be done to improve medical…
The National Center for Complementary and Integrative Health (NCCIH) has launched an app that is designed to inform people about the science behind herbs and herbal supplements commonly marketed for…
A married couple from Grimsby in England are planning to undergo kidney transplant surgery. Paula will donate her kidney to her husband Kevin, who has polycystic kidney disease. The original…
Novartis has teamed up with Numinous Games to develop Galaxies of Hope, an app that is designed to support the neuroendocrine tumour (NET) community. You can read the original source…
Jaiden, a twelve-year-old boy, has been diagnosed with stiff skin syndrome, a rare disease that causes his skin to harden. His family has been sharing their experiences with the condition.…
Researchers from the University of Illinois have been studying the effects of endocannabinoids (a type of molecule that occurs naturally in the body) on cancer. So far, the researchers have…
A drug to treat prostate cancer has been approved by the US Food and Drug Administration. The drug, Xtandi ® (enzalutamide), had previously been approved for castration-resistant prostate cancer (CRPC)…
The biotechnology company Philogen S.p.A. has announced that the US FDA has awarded Orphan Drug status to Daromun for the treatment of stages IIb to IV melanoma. The original media…
Colin Wells, an actor who has previously played roles in the TV shows Hollyoaks and Casualty, has a son and daughter who are both diagnosed with mitochondrial disease. The source…
The organisations Guerbet and IBM Watson Health are collaborating to develop an artificial intelligence tool designed to support the diagnosis and care of liver cancer. The source article can be…
A patient with Waldenström Macroglobulinemia taking part in a clinical trial of the experimental drug CLR 131 for the treatment of B-cell hematologic cancers is reported to have achieved a…
Clovis Oncology, Inc. has announced that they have submitted an application to the European Medicines Agency (EMA). The application is to extend the drug Rubraca’s®(rucaparib) marketing authorisation to include maintenance…
CannTrust Holdings Inc. and Australia’s Gold Coast University Hospital will work together to carry out a clinical trial. The study will evaluate CannTrust’s cannabidiol oil capsules as a way to…
The National Health Service (NHS) England is facing criticism following their decision not to fund the drug everolimus as a treatment for tuberous sclerosis complex associated refractory epilepsy. In comparison,…
MedicNova Inc. has announced the results of subgroup analyses after a finished clinical trial. The trial was designed to evaluate MN-166 (ibudilast) as a possible treatment for amyotrophic lateral sclerosis…
A recent review, carried out by researchers from Spain and published in the Orphanet Journal of Rare Diseases (OJRD), discusses the rare condition alpha-1 antitrypsin deficiency. The original study, which…
The U.S. Food and Drug Administration (FDA) has just approved a treatment for smallpox. According to the World Health Organisation, there hasn’t been a known natural infection from smallpox since…
A recent study, published here in the journal Nature Medicine and used as the source for this article, has found that certain kinds of cells may be useful for predicting…
An experimental gene therapy program (called AXO-AAV-OPMD) being developed for the treatment of oculopharyngeal muscular dystrophy has been licensed with exclusive global rights to Axovant Sciences from Benitec Biopharma. There…
Zogenix, Inc has announced the top-line results from a Phase 3 study of the investigational drug ZX008 (low-dose fenfluramine hydrochloride) for the treatment of young patients with Dravet syndrome. The…
Zynerba Pharmaceuticals, Inc. has announced their plans to begin a clinical trial of Cannabidiol in children and teenagers who have Fragile X syndrome. The study, called CONNECT-FX, is expected to…
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