Anna is from England and recently finished her undergraduate degree. She has an interest in medicine and enjoys writing. In her spare time she likes to cook, hike, and hang out with cats.
Dova Pharmaceutics has submitted a supplemental New Drug Application to the US FDA on behalf of Doptelet® (avatrombopag), which is being researched as an investigational treatment of immune thrombocytopenia in…
The medical company Biogen has announced that the first patient has been enrolled in a Phase 3 clinical trial investigating a drug as a potential treatment for severe cerebral edema…
A recent study using mice suggests that Huntington’s disease may begin to show symptoms early on in life. For more detailed information, you can read the source article here, at…
The US Department of Labor has shared an opinion letter that protects the job security of eligible living organ donors who need to take time off for their donation. For…
The US Food and Drug Administration and Eiger BioPharmaceuticals, Inc. have met to discuss lonafarnib, a drug being investigated as a potential treatment for Hutchinson-Gilford Progeria Syndrome. For more detailed…
Doctors in Britain are being urged to write outpatient clinic letters in plain English and address them to their patients, rather than using technical medical language written to the patient’s…
Researchers are looking for participants to take part in a study investigating whether a mobile app could benefit patients with multiple sclerosis. For more information about this study and how…
Initial results from a clinical trial investigating the effects of an experimental drug called BCX7353 in patients with hereditary angioedema suffering from acute attacks. For more detailed information, you can…
Cynata Therapeutics, an Australian stem cell and regenerative medicine company, has announced positive results from a Phase 1 clinical trial of CYP-001, the CymerusTM mesenchymal stem cell product candidate. The study…
The US Food and Drug Administration has approved a drug called TakhzyroTM (lanadelumab-flyo) for the treatment of hereditary angioedema. This approval was based on supporting evidence from several studies, including from…
The information in this article is sourced from this leaflet from Frambu and this publication from Eurordis. You can also visit Frambu’s website by clicking here. Frambu is a national centre…
A recent study carried out by researchers from the University of Copenhagen has developed a new method that may have the potential to diagnose many different types of cancers early…
According to a recent press release, Pfizer Inc. has terminated two on-going clinical trials that were investigating domagrozumab (PF-06252616) as a potential treatment for Duchenne muscular dystrophy. This decision follows…
The company Imago Biosciences, which focuses on developing anti-cancer therapies, is carrying out a Phase 1/2a clinical study of an investigational drug called IMG-7289 as a potential treatment for…
1LifeMax Laboratories, Inc. has announced that they have entered into an agreement with Novartis Pharma AG that gives them an exclusive worldwide license for an investigational drug called BPR277. LifeMax…
A recent article published in the journal Sleep Review explores why some people with sleep apnea may still experience sleepiness after treatment, and suggests that it may be linked to…
The US FDA has approved the first drug to treat neurotrophic keratitis, a degenerative condition that affects the eyes. Approval of the drug, called Oxervate (cenegermin), is granted to…
A team of researchers from the University of North Carolina have been exploring an experimental method of delivering drugs to medulloblastoma that involves converting skin cells into stem cells that…
Reflection Biotechnologies has announced that the US Food and Drug Administration has awarded Orphan Drug Designation to their RBIO-101 program, which is focused on a gene therapy designed to treat…
The United States government has awarded a grant of over $4 million to fund research into genetic mitochondrial diseases. The three-year grant was given to the Children’s Hospital of Philadelphia…
A recent study, carried out by researchers from the National Cancer Institute (part of the NIH) and several other universities, outlines a potential new method of predicting whether immune checkpoint…
Pfizer has released the primary results from the Phase 3 clinical trial of tafamidis, an investigational drug being researched as a potential treatment for transthyretin amyloid cardiomyopathy. For more…
The Australian biopharmaceutical company Antisense Therapeutics has announced that the first patient has been dosed on a Phase 2 clinical trial of the investigational drug ATL1102, which is being developed…
The United States Adopted Name Council, which selects simple, new, and informative generic drug names, has approved ‘Onvansertib’ as the generic name for PCM-075. PCM-075 is an investigational drug that…
A research team, funded in part by grants from the NIH and the National Multiple Sclerosis Society, say that they have discovered a new subtype of multiple sclerosis. The…
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