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Congenital Athymia

Home » Congenital Athymia
Rethymic FDA-Approved for Congenital Athymia
source: pixabay.com

Rethymic FDA-Approved for Congenital Athymia

  • Post author:Jessica Lynn
  • Post published:October 12, 2021
  • Post category:Congenital Athymia

Prior to October 8, 2021, there were no FDA-approved treatment options for pediatric patients with congenital athymia, an ultra-rare immune disorder. However, this all changed when the FDA approved Rethymic…

Continue Reading Rethymic FDA-Approved for Congenital Athymia
Novel Investigative Therapy for Pediatric Congenital Athymia Submitted to FDA for Approval

Novel Investigative Therapy for Pediatric Congenital Athymia Submitted to FDA for Approval

  • Post author:Trudy Horsting
  • Post published:June 2, 2021
  • Post category:Congenital Athymia

Enzyvant has just announced that they have resubmitted their application of RVT-802 to the FDA as a therapy for pediatric congenital athymia. Their first application was submitted in 2019. The…

Continue Reading Novel Investigative Therapy for Pediatric Congenital Athymia Submitted to FDA for Approval
New Normals and Athymia Advocacy: Part 2 of Aunika’s Story

New Normals and Athymia Advocacy: Part 2 of Aunika’s Story

  • Post author:Rebekah
  • Post published:September 18, 2019
  • Post category:Congenital Athymia/Immune defect due to absence of thymus/Rare Disease

Click here for Part 1 of Aunika's Story Despite the success of the transplant, baby Aunika wasn’t out of the woods yet. She continued to have issues with breathing and…

Continue Reading New Normals and Athymia Advocacy: Part 2 of Aunika’s Story

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