Spinal muscular atrophy type I with congenital bone fractures Archives

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Risdiplam Delivers An Improvement to Infants with Spinal Muscular Atrophy Type 1

Post author:Rose Duesterwald
Post published:January 29, 2020
Post category:Adult-onset spinal muscular atrophy Spinal muscular atrophy type I with congenital bone fractures

Genentech (Roche Group) announced positive results of its FIREFISH trial in a recent Business Wire news release. The second part of the study evaluated risdiplam’s efficacy on infants ages one…

Clinical Trials Show Promising Results for Risdiplam in Treatment of Spinal Muscular Atrophy Types 1, 2, and 3

Post author:Rose Duesterwald
Post published:October 9, 2019
Post category:Adult-onset spinal muscular atrophy Spinal Muscular Atrophy Spinal muscular atrophy type I with congenital bone fractures

According to a recent article in SMA News Today, risdiplam (formerly RG7916) is in ongoing studies of patients with spinal muscular atrophy (SMA). The drug is an investigational medicine developed by Genentech…

New Drug Under Review by the FDA to Treat the Most Lethal Form of Spinal Muscular Atrophy

Post author:Rose Duesterwald
Post published:April 30, 2019
Post category:Spinal Muscular Atrophy Spinal muscular atrophy type I with congenital bone fractures

According to an article in Biospace, the FDA is currently reviewing data from the Phase III STRIVE clinical trial for possible approval of Zolgensma as gene therapy for spinal…

Risdiplam Delivers An Improvement to Infants with Spinal Muscular Atrophy Type 1

Clinical Trials Show Promising Results for Risdiplam in Treatment of Spinal Muscular Atrophy Types 1, 2, and 3

New Drug Under Review by the FDA to Treat the Most Lethal Form of Spinal Muscular Atrophy

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