
FDA Unveils New Framework for Rare Disease Drug Approvals: More Structure, Uncertain Benefits
Bree Clare - September 12, 2025LISTEN TO OUR PODCAST
THE LATEST FROM PATIENT WORTHY
FEATURED
UPCOMING EVENTS
SIGN UP FOR OUR NEWSLETTER
Hemophilia B affects far more than just how long it takes to stop a cut. From hidden internal bleeds to unexpected complications, its impact often goes unseen and untreated for far too long. Swipe through to understand how this condition works, how severity is measured, and why recognizing the signs matter more than you might think! #hemophiliab #raredisease #shareyourstory #PatientWorthy
If you're interested in sharing your story, click here: bit.ly/4dV7gru
... See MoreSee Less




- likes 1
- Shares: 0
- Comments: 0
The FDA has revealed new framework for approval processes tied to rare disease treatments. Read more here:
patientworthy.com/2025/09/12/fda-unveils-new-framework-for-rare-disease-drug-approvals-more-struc...
... See MoreSee Less

This #FactFriday for PCOS Awareness Month, we’re sharing facts to help you better understand polycystic ovary syndrome—from its wide range of symptoms to its impact on long-term health. Share to support early diagnosis, break stigma, and empower those affected! #PCOSAwarenessMonth #PCOS #PolycysticOvarySyndrome #WomensHealth #FactFriday #PatientWorthy
#ShareYourStory with us here: bit.ly/4dV7gru
... See MoreSee Less



