Lord Julian Fellowes, the Oscar-winning creator of Downton Abbey, has undergone a transformative treatment for essential tremor (ET) using Insightec’s magnetic resonance-guided focused ultrasound (MRgFUS)
My story is like so many other’s stories: healthy, semi-young, active, usually chose the salad over the fries, parked farther away in the parking lot
Over 9,300 individuals living in the United States are currently waiting for a liver transplant. There is a serious need for liver donors. This message
Narcolepsy is a chronic neurological disorder that disrupts the brain’s ability to regulate the sleep-wake cycle, causing a profound impact on daily life. Characterized by
Editor’s Note: We’re proud to be the first to share this story by Blair Young Whitworth, a Parent Champion of the Courageous Parents Network. There
The U.S. Food and Drug Administration (FDA) has granted Fast Track designation to SAR402663, Sanofi’s investigational gene therapy for neovascular age-related macular degeneration (AMD). As
Coffee lovers have long celebrated their favorite beverage for its taste and energy boost, but recent research offers another compelling reason to savor that daily
I came to the United States from the Philippines in June 2016, full of excitement and dreams. I was ready to build a new life,
An experimental gene therapy known as AMT-130 has become the first treatment to successfully slow the progression of Huntington’s disease, marking a potential breakthrough in
Lexeo Therapeutics announced a significant regulatory development this week: the U.S. Food and Drug Administration (FDA) is open to a faster approval pathway for the
Editor’s Note: Patient Worthy is proud to share this story from our friends at the Glanzmann’s Research Foundation (GRF). To see the article in its
Your story has the power to educate, motivate, and make a real difference in the lives of others. We are looking for patients with Metabolic
Your story has the power to educate, motivate, and make a real difference in the lives of others. We are looking for patients with Metabolic
In a groundbreaking international effort led by Dr. Shady Rahayel of Université de Montréal and reported by MSN.com, researchers have discovered new ways to predict
AstraZeneca and Daiichi Sankyo have announced promising Phase 3 trial results for Datroway, their investigational antibody-drug conjugate (ADC) targeting triple-negative breast cancer (TNBC). The trial
Bayer AG and its subsidiary BlueRock Therapeutics LP have announced encouraging 36-month follow-up data from the Phase I exPDite clinical trial of bemdaneprocel (BRT-DA01), an
Editor’s Note: Patient Worthy is proud to bring you this story from our friends at the Glanzmann Research Foundation. To see the article in its
Clinical trials often begin with optimism, sites are launched, projections look promising, and timelines are set. But when enrollment stalls, sponsors frequently call-in patient recruitment
Transthyretin amyloid cardiomyopathy (ATTR-CM) happens when a protein called TTR builds up in the heart, making it harder to pump blood. It can cause fatigue, swelling, or shortness of breath but these symptoms are easy to mistake for something else.
That’s why stories and awareness matter! The more people who recognize the signs, the more likely it is to get caught early. If you're interested in sharing your story, click here: bit.ly/4dV7gru
#ATTRCM #AmyloidosisAwareness #HeartHealth #RareDisease #ShareYourStory #PatientWorthy
Did you know? Combined Small-Cell Lung Carcinoma (C-SCLC) blends features of two major lung cancer types within the same tumor. Let’s use Lung Cancer Awareness Month to spread knowledge and support everyone affected by rare lung cancers. #LungCancerAwarenessMonth #RareLungCancer #CSCLC #LungCancer #PatientWorthy
#ShareYourStory with us here: bit.ly/4dV7gru
A new ALS drug has begun accelerated development after a surge in early-stage clinical activity. Read more here:
patientworthy.com/2025/11/11/als-drug-development-accelerates-spotlight-on-medicinovas-mn-166/
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