Charcot Marie Tooth disease type1A

source: pixabay.com

An Investigative Therapy for Charcot-Marie-Tooth Disease Type 1A has Shown Lasting Results

Post author:Trudy Horsting
Post published:February 10, 2020
Post category:Charcot-Marie-Tooth disease Rare Disease

Phase 3 Trial A Phase 3 trial run by Pharnext examining the safety and the efficacy of an investigative therapy called PXT3003 began in December of 2015. It enrolled 323…

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