October 2018 is the Expected Date for Top-Line Results From a Phase 3 Trial of an Experimental Treatment for Charcot-Marie-Tooth Disease
<a href="https://pixabay.com/users/mohamed_hassan/">mohamed_hassan</a> / Pixabay

October 2018 is the Expected Date for Top-Line Results From a Phase 3 Trial of an Experimental Treatment for Charcot-Marie-Tooth Disease

An ongoing Phase 3 clinical trial program is investigating the drug PXT3003 as an experimental treatment for Charcot-Marie-Tooth disease type 1A in adults. Pharnext SA says that they expect to…

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Editor’s Choice: Staying Strong, Fighting for Treatment, and Feeling Vulnerable- Just Another Day in the Life of Rare Patients

Happy Father's Day Weekend Patient Worthians! This week we have an amazing essay written by CMT Warrior Sarah Magno regarding her personal experience overcoming rare disease obstacles. We also have some…

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