By engineering exosomes, Sarepta Therapeutics believes they can utilize gene therapies, RNA therapies, and gene editing without triggering an immune response in the body. They have just announced a new…
According to a story from PR Newswire, CureDuchenne Ventures has recently announced the initiation of its CureDuchenne Ventures 2020 Pitch Contest. This marks the first time that the contest has…
Parent Project Muscular Dystrophy is a nonprofit that aims to find a cure for Duchenne muscular dystrophy. One of their programs, the Certified Duchenne Care Center Program (CDCCP), has recently…
CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families May 30th, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…
CureDuchenne Cares Workshops: Hear The Latest From Experts May 16th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…
CureDuchenne Cares Workshops: Hear The Latest From Experts May 2nd, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…
According to a story from the CureDuchenne Blog, CureDuchenne founder and CEO Debra Miller announced that the organization has recently entered into a new partnership with the biotechnology company Myosana…
by Jodee Redmond from In The Cloud Copy Rich Horgan is the founder of the Boston-based biotech non-profit, Cure Rare Diseases. The 28-year-old decided to take action over concerns about…
CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families April 25th, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…
CureDuchenne Cares Workshops: Hear The Latest From Experts April 18th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…
As originally discussed in Muscular Dystrophy News Today, a recent study has discovered that increasing levels of utrophin in the body can improve muscle strength, form, and function for patients…
According to a study published in the journal Neurology, a measure called the vastus lateralis fat fraction was found to be useful in predicting the age at which a patient living…
CureDuchenne Cares Workshops: Hear The Latest From Experts April 4th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…
According to a story from CureDuchenne, the biotechnology company Dyne Therapeutics recently announced that CureDuchenne Ventures has made an equity investment that will support the development of all new precision…
CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families March 28th, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…
CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families March 21st, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…
A Professional Course for Healthcare Providers This course meets all Montana Board of PT requirements for 6.5 CE hours and is approved by the Montana Board of OT Practice. The…
CureDuchenne Cares Workshops: Hear The Latest From Experts March 14th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…
CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families March 7th, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…
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Advances in medicine have been responsible for longer overall survival in patients with neurodegenerative-neuromuscular diseases. According to a recent report in RTMagazine, an increase in the number of patients…
CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families February 22nd, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…
AskBio Asklepios BioPharmaceuticals (AskBio) was first founded in 2001. It is based out of North Carolina. This company is dedicated to the research of gene therapies as potential therapeutic options…
A Professional Course for Healthcare Providers This course has been verified by the Texas PT for 6.5 CCUs. The professional course is a valuable opportunity for caregivers and healthcare providers…
CureDuchenne Cares Workshops: Hear The Latest From Experts February 8th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…
PTC Therapeutics is a pharmaceutical company that has been working with Translarna, a medication intended for the treatment of Duchenne muscular dystrophy (DMD). They analyzed this treatment and presented the…
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