Fast Track Designation Granted for Gene Therapy Treatment of Duchenne Muscular Dystrophy
source: pixabay.com

Fast Track Designation Granted for Gene Therapy Treatment of Duchenne Muscular Dystrophy

by Lauren Taylor from In The Cloud Copy Duchenne muscular dystrophy (DMD) is a rare genetic condition that ultimately leads to the wasting away of muscles over time. The condition…

Continue Reading Fast Track Designation Granted for Gene Therapy Treatment of Duchenne Muscular Dystrophy

CureDuchenne Cares Session: Honolulu, HI

  • Post author:
  • Post category:

CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families August 22nd, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…

Continue Reading CureDuchenne Cares Session: Honolulu, HI
Duchenne Muscular Dystrophy: Two Patients with a Rare Mutation Were Just Dosed with Gene Therapy
source: pixabay.com

Duchenne Muscular Dystrophy: Two Patients with a Rare Mutation Were Just Dosed with Gene Therapy

According to a story from the CureDuchenne Blog, Dr. Kevin Flanigan of Nationwide Children's Hospital has recently dosed two Duchenne muscular dystrophy patients with an experimental gene therapy. This gene…

Continue Reading Duchenne Muscular Dystrophy: Two Patients with a Rare Mutation Were Just Dosed with Gene Therapy
A New Partnership will Advance Exosome-Based Gene Therapy for Neuromuscular Diseases
source: pixabay.com

A New Partnership will Advance Exosome-Based Gene Therapy for Neuromuscular Diseases

By engineering exosomes, Sarepta Therapeutics believes they can utilize gene therapies, RNA therapies, and gene editing without triggering an immune response in the body. They have just announced a new…

Continue Reading A New Partnership will Advance Exosome-Based Gene Therapy for Neuromuscular Diseases

CureDuchenne Cares Session: Omaha, NE

  • Post author:
  • Post category:

CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families May 30th, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…

Continue Reading CureDuchenne Cares Session: Omaha, NE

CureDuchenne Cares Workshop: Manhattan, NY

  • Post author:
  • Post category:

CureDuchenne Cares Workshops: Hear The Latest From Experts May 16th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…

Continue Reading CureDuchenne Cares Workshop: Manhattan, NY

CureDuchenne Cares Workshop: Birmingham, AL

  • Post author:
  • Post category:

CureDuchenne Cares Workshops: Hear The Latest From Experts May 2nd, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…

Continue Reading CureDuchenne Cares Workshop: Birmingham, AL
CureDuchenne Announces Partnership with Myosana Therapeutics for Duchenne Muscular Dystrophy Treatment
source: pixabay.com

CureDuchenne Announces Partnership with Myosana Therapeutics for Duchenne Muscular Dystrophy Treatment

According to a story from the CureDuchenne Blog, CureDuchenne founder and CEO Debra Miller announced that the organization has recently entered into a new partnership with the biotechnology company Myosana…

Continue Reading CureDuchenne Announces Partnership with Myosana Therapeutics for Duchenne Muscular Dystrophy Treatment
Boston Man Tackling Duchenne Muscular Dystrophy Cure After Sibling’s Diagnosis
source: pixabay.com

Boston Man Tackling Duchenne Muscular Dystrophy Cure After Sibling’s Diagnosis

by Jodee Redmond from In The Cloud Copy Rich Horgan is the founder of the Boston-based biotech non-profit, Cure Rare Diseases. The 28-year-old decided to take action over concerns about…

Continue Reading Boston Man Tackling Duchenne Muscular Dystrophy Cure After Sibling’s Diagnosis

CureDuchenne Cares Session: Baltimore, MD

  • Post author:
  • Post category:

CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families April 25th, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…

Continue Reading CureDuchenne Cares Session: Baltimore, MD

CureDuchenne Cares Workshop: San Diego, CA

  • Post author:
  • Post category:

CureDuchenne Cares Workshops: Hear The Latest From Experts April 18th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…

Continue Reading CureDuchenne Cares Workshop: San Diego, CA

CureDuchenne Cares Workshop: Sacramento, CA

  • Post author:
  • Post category:

CureDuchenne Cares Workshops: Hear The Latest From Experts April 4th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…

Continue Reading CureDuchenne Cares Workshop: Sacramento, CA
New Equity Investment Aims to Develop New Duchenne Muscular Dystrophy Drug
source: pixabay.com

New Equity Investment Aims to Develop New Duchenne Muscular Dystrophy Drug

According to a story from CureDuchenne, the biotechnology company Dyne Therapeutics recently announced that CureDuchenne Ventures has made an equity investment that will support the development of all new precision…

Continue Reading New Equity Investment Aims to Develop New Duchenne Muscular Dystrophy Drug

CureDuchenne Cares Sessions: Boston, MA

  • Post author:
  • Post category:

CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families March 28th, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…

Continue Reading CureDuchenne Cares Sessions: Boston, MA

CureDuchenne Cares Session: Billings, MT

  • Post author:
  • Post category:

CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families March 21st, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…

Continue Reading CureDuchenne Cares Session: Billings, MT

CureDuchenne Cares Workshop: Phoenix, AZ

  • Post author:
  • Post category:

CureDuchenne Cares Workshops: Hear The Latest From Experts March 14th, 2020, 8:00 am The Workshops program from CureDuchenne are day-long educational events that are oriented towards caregivers and Duchenne muscular…

Continue Reading CureDuchenne Cares Workshop: Phoenix, AZ

CureDuchenne Cares Session: Knoxville, TN

  • Post author:
  • Post category:

CureDuchenne's Cares Sessions: Helping Connect and Inform Patient Families March 7th, 2020, 6:30 pm The Sessions program from CureDuchenne is geared specifically towards patients and their families as well as…

Continue Reading CureDuchenne Cares Session: Knoxville, TN
Neurodegenerative-Neuromuscular Diseases and Airway Clearance Therapy
source: pixabay.com

Neurodegenerative-Neuromuscular Diseases and Airway Clearance Therapy

  Advances in medicine have been responsible for longer overall survival in patients with neurodegenerative-neuromuscular diseases. According to a recent report in RTMagazine, an increase in the number of patients…

Continue Reading Neurodegenerative-Neuromuscular Diseases and Airway Clearance Therapy