Imagine that your loved one is diagnosed with a rare disease. The first thing you do is to go to the internet to understand what you can about this disease…
Accessing treatments can be difficult, especially if one is impacted by a rare disease. In fact, only 5% of rare diseases have an FDA-approved treatment. Because of this, many patients…
In March 2021, the FDA expanded access approval to biotechnology company Longeveron Inc.'s investigational Lomecel-B to a pediatric patient with hypoplastic left heart syndrome (HLHS). According to a press…
Discussion on Right to Try legislation continues, and the federal government could soon change existing rules. Many people wonder whether or not patients should have the right to try potentially…
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