Initially, when doctors in Malaysia met with the 21-year-old patient, they suspected that he had mandibuloacral dysplasia. The man, 21 years old, was short in stature (3.8 ft tall)…
Parents of children who have received a diagnosis of Hutchinson-Gilford progeria syndrome (HGPS) may be relieved to learn the FDA recently approved Zokinvy capsules that were developed to lower…
As of November 20, Zokinvy has been approved by the FDA for the treatment of Hutchinson-Gilford progeria syndrome (progeria) and a few other progeroid laminopathies in patients aged one year…
According to a publication from Pharmaceutical Technology, California-based Eiger Biopharmaceuticals is preparing to submit a New Drug Application (NDA) to the Food and Drug Administration (FDA) for their experimental progeria…
The US Food and Drug Administration and Eiger BioPharmaceuticals, Inc. have met to discuss lonafarnib, a drug being investigated as a potential treatment for Hutchinson-Gilford Progeria Syndrome. For more detailed…
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