Researchers and scientists have stated that it can be difficult to diagnose and treat patients with mucinous ovarian cancer. In fact, because the cancer is often not found until it…
Each day, an estimated five children within the U.S. are born with congenital diaphragmatic hernia (CDH), a diaphragmatic defect which is fatal in approximately 33% of cases. While these hernias…
It’s no secret that more mathematics, data, and technology are being used to drive advances within healthcare and medicine. For example, we’ve seen the heightened use of artificial intelligence (AI)…
What is the underlying cause of cancers such as esophageal adenocarcinoma or intestinal gastric cancer? Are there certain precursor cells that these cancers arise from? According to a news release…
More rare conditions are discovered as we learn more about the human body and genetics. For example, shares an article in Medical XPress, a research team from the University of…
Clinical trials play a crucial role in better understanding rare diseases and therapeutic interventions. According to a news release from rare disease company Albireo Pharma, Inc. (“Albireo”), enrollment is now…
Oxytocin has been deemed the "love drug" or "love hormone." This hormone, which controls aspects of behavior and reproduction, is often released when we're in love or in physical…
According to a late October 2022 news release from gene therapy company AVROBIO, the sixth patient has been dosed in a Phase 1/2 clinical study evaluating AVR-RD-04 for patients…
The European Society for Gene and Cell Therapy (ESGCT) recently held its Annual Congress from October 11-14, 2022. During the ESGCT Congress, various stakeholders discussed data, trends, and new research…
Glioblastoma multiforme (GBM) is notoriously difficult-to-treat. This cancer is both aggressive and invasive, spreading “tentacles” and becoming hard to remove even with surgery. As a result, finding more effective therapeutic…
Glioblastoma is notoriously difficult to treat and manage. The cancer is not only aggressive and quickly spreading, but is often treatment-averse. Because of this, glioblastoma comes with a poor prognosis…
For the last few decades, there has been increased interest in understanding the effects of sleep (or lack of!) on our overall health. A recent study sought to understand the…
Unfortunately, there are no cures - nor effective treatment options - for individuals with P-subtype small cell lung cancer (SCLC). This subtype is notoriously treatment-averse; it is also relatively…
When the COVID-19 pandemic began, many people wondered how it would impact them, especially if living with a rare disease or condition. As the pandemic has progressed, more research has…
Unfortunately, not much is understood still about chronic traumatic encephalopathy (CTE). However, we do know that it has been linked to repeated head trauma or head injury, such as that…
According to a news release on Yahoo! Finance, clinical-stage biotechnology company Freeline Therapeutics Holdings plc ("Freeline") shared that it had initiated dosing in the second cohort of the Phase…
According to a late September 2022 news release from biopharmaceutical company AEON Biopharma, Inc., positive topline data is available from a clinical trial evaluating ABP-450 for patients with cervical…
Did you know that bone mass accrual and bone mineral density depend highly on puberty? Because of this, puberty delays or interruptions can negatively affect bone mineral density or cause…
In an October 13, 2022 news release from biotechnology company INOVIO, the company shared that positive interim data was available from a Phase 1/2 study. Within the study, researchers…
It’s no secret that excess alcohol consumption can result in numerous adverse health effects. According to an article in the Pharmacy Times, researchers sought to understand how excess alcohol…
Currently, treatment options for Williams syndrome are considered symptomatic; they treat symptoms of the condition, but not the underlying cause. There are no treatments or cures addressing the underlying genetic…
What is the best therapeutic option for individuals with atrial fibrillation (AF or AFib) and chronic kidney disease (CKD)? Currently, doctors typically recommend direct oral anticoagulants (DOACs) to patients with…
Enzyme replacement therapy (ERT) is an approved treatment strategy for those with Pompe disease. It involves providing patients with alpha-glucosidase, which helps to break down glycogen. In addition to reducing…
Oral corticosteroid drugs can help treat Bell’s palsy, a condition which causes temporary facial weakness or paralysis, if the muscles remain paralyzed over time. According to News Medical, researchers…
According to an article from Marisa Wexler in Muscular Dystrophy News, promising study data is available from the Phase 1 ARCH study. Within the study, researchers evaluated EDG-5506, an…
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