Updates on Gene Therapy Research for Rare Diseases During the COVID-19 Pandemic

Research During COVID Many medical research projects have faced hurdles since the pandemic has started. Regulators have changed development timelines, and many have had to delay their clinical trials due…

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Survey Indicates Needs of Rare Disease Patients During COVID-19
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Survey Indicates Needs of Rare Disease Patients During COVID-19

Eurordis The European Organization for Rare Diseases (Eurordis) is a nonprofit organization which organizes over 930 rare disease groups into one alliance. Groups have joined the network from 73 different countries.…

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New Potential Therapy to Treat Pulmonary Fibrosis in Systemic Sclerosis and COVID-19
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New Potential Therapy to Treat Pulmonary Fibrosis in Systemic Sclerosis and COVID-19

Pulmonary fibrosis is a condition that is caused by scarring of the lungs which can lead to shortness of breath and other respiratory issues. Some cases of COVID-19 have lead to…

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Patients with Rare Autoimmune Rheumatic Disease Face More Severe COVID-19 Cases

A review of COVID-19 data from the UK shows that patients with rare autoimmune rheumatic disease (RAIRD) face a higher mortality risk, according to an article in Healio. The study,…

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Study Examines Telehealth Visits for Patients with Autoimmune Conditions During COVID-19

Michael George and his team from the University of Pennsylvania have recently uncovered new insights regarding autoimmune patient’s comfortability with care during COVID-19. They've been working since the pandemic began…

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Phase 1 LYT-100 Study Shows Promise for IPF, Lymphedema
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Phase 1 LYT-100 Study Shows Promise for IPF, Lymphedema

Recently, biotherapeutics company PureTech Health announced that their Phase 1 trial to evaluate LYT-100 (deupirfenidone) has completed. During the multiple ascending dose and food effect study, researchers analyzed the safety,…

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The FDA Found Issue With Several NDAs in 2020, Partly Due to the COVID-19 Pandemic

COVID-19’s tentacles have invaded the New Drug Applications (NDAs) for 2020. A recent article in Fierce Pharma reported that the FDA has been especially vigilant in scrutinizing NDAs this year,…

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Charcot-Marie-Tooth Disease Patients Report Declines During COVID-19 Lockdown
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Charcot-Marie-Tooth Disease Patients Report Declines During COVID-19 Lockdown

According to a story from Charcot-Marie-Tooth News, patients living with Charcot-Marie-Tooth disease have reported in a recent survey that their symptoms of pain and decline in mobility increased during the…

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His Son was Taken Off the Shield List, and Now They Feel Unprotected from COVID-19
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His Son was Taken Off the Shield List, and Now They Feel Unprotected from COVID-19

As reported in the BBC; Aaron Bradley is concerned that returning to work will endanger his son’s health. This follows the Scottish governments decision to move his toddler off of…

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CureVac Joins the Race to Develop a Vaccine Against COVID-19 With Its Successful Phase 1 Trial

According to an article in Biospace, CureVac of Boston, MA, with headquarters in Tübingen, Germany, just announced interim results from its Phase 1 study evaluating CVnCoV, a vaccine candidate against…

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