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How Well Do Market Drugs Fare?
Source: Pixabay

How Well Do Market Drugs Fare?

  • Post author:Andres Rovira
  • Post published:December 13, 2017
  • Post category:MPS IV (Morquio syndrome)/Rare Disease

Back in 2014, the FDA gave the green light for eight brand new drugs for orphan diseases. Among the pack was BioMarin Pharmaceutical's very own VimiZim. Weird name right? Well,…

Continue Reading How Well Do Market Drugs Fare?
Morquio Syndrome: How One Inspirational Man Refused to Take “No” for an Answer
[Source: pixabay.com]

Morquio Syndrome: How One Inspirational Man Refused to Take “No” for an Answer

  • Post author:Alisha Stone
  • Post published:February 8, 2017
  • Post category:MPS IV (Morquio syndrome)/Rare Disease

I have a new hero, an Irishman who’s not only gotten some great press and notoriety, this guy has struck gold in the hearts of the Morquio syndrome community! In…

Continue Reading Morquio Syndrome: How One Inspirational Man Refused to Take “No” for an Answer
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