First Treatment in China for Morquio A Syndrome Earns Approval
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First Treatment in China for Morquio A Syndrome Earns Approval

According to a story from Market Screener, the biotechnology company BioMarin Pharmaceutical Inc. recently announced that the Chinese government has approved the company's drug elosulfase alfa (marketed at Vimizim) as…

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Research Suggests a Multiple Sclerosis Treatment May Also Benefit Mucolipidosis IV
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Research Suggests a Multiple Sclerosis Treatment May Also Benefit Mucolipidosis IV

Researchers at the Massachusetts General Hospital Research Institute and the Georgia Institute of Technology are investigating a medication currently approved to treat a type of multiple sclerosis as a possible…

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Satellite Symposium Discusses Long-Term Outcomes for MPS IVA and VI Patients
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Satellite Symposium Discusses Long-Term Outcomes for MPS IVA and VI Patients

Yesterday, a group of experts presented "Changing lives: Long-term outcomes of MPS IVA & VI patients" at the Satellite Symposium sponsored by BioMarin. The program began with insights on the…

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Is This What the MPS Research Community Been Missing?
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Is This What the MPS Research Community Been Missing?

Recent findings from research done at the University of Pennslyvania indicate a new biomarker associated with a group of rare metabolic diseases called mucopolysaccharidoses (MPS). A biomarker is a measurable…

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Morquio Syndrome: How One Inspirational Man Refused to Take “No” for an Answer
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Morquio Syndrome: How One Inspirational Man Refused to Take “No” for an Answer

I have a new hero, an Irishman who’s not only gotten some great press and notoriety, this guy has struck gold in the hearts of the Morquio syndrome community! In…

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