It's Guacher Disease Awareness Month! According to eurogaucher.org, International Gaucher Day was a success! This year it was observed on October 1st to bring awareness to Gaucher disease. The European Gaucher…
According to a late-summer press release sent out by the companies, two pharma players are joining forces and making waves in gene therapy for hemophilia A. Sangamo and Pfizer announce…
David Church is a 21-year-old Professional Billiards player and he has the will power of a Saint. He suffers from Moebius syndrome, an extremely rare neurological disorder that causes severe…
At first glance, little Victoria Thompson looks like your average happy and healthy toddler. You'd have no idea that once upon a time, she had a tumor on her kidney…
Every year, hundreds of people in America are infected with babesiosis, a tick-borne infection that causes malaria-like symptoms. For some reason, older white men have the highest rates of infection.…
Rare disease research can feel like an uphill battle. First of all, rare diseases have a harder time receiving funding. After that, it takes months or even years to have…
Let's talk medical foods, shall we? For those of you who haven't heard of them, a medical food is a food that is created in order to be eaten or…
The memories we have of growing up should be the type that we look back on and smile about. That is not to say that they all should be happy…
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