The Lewis family has lived through it all. Their first born was diagnosed with spinal muscular atrophy (SMA) and did not live long, having passed away in 2013, reports Deseret News. And…
The O'Sullivan family had three very healthy babies before Drake was born. His blue eyes energetically said hello and his weight met all health standards, yet it wasn't until three…
According to an article from Parkinson's News Today, a recent analysis testing transcranial magnetic stimulation demonstrated that the procedure was not effective in treating the depression that is a common…
According to a story from the Irish Mirror, eleven year old Cezy Fosca, who has a rare condition called Morquio syndrome, has lost access to the only drug available that…
According to a story from the Vancouver Sun, five rare disease drugs just received coverage in British Columbia. The funding comes from savings accumulated thanks to a recent agreement that…
According to a story from news-medical.net, a recent study that the reduced expression of miR-125a-5p results in an increase in the concentration of the protein TIMP-1. Prior research has associated…
A new digital platform has been created with hopes to assist cystic fibrosis (CF) patients at the comfort of their own homes, limiting hospital visits, reports Evening Standard. This new…
Originally reported by The Jerusalem Post, many adopted children from Eastern European countries suffer from fetal alcohol spectrum disorder caused by their mothers drinking alcohol excessively when pregnant. Many Israelis families…
According to an article from globenewswire.com, the pharmaceutical company Amicus Therapeutics announced that the Food and Drug Administration (FDA) has the company's New Drug Application for migalastat with filing for…
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