August 20, 2018 - Patient Worthy

FDA Grants Orphan Drug Designation to Onspira Therapeutics’ Investigational Interleukin-1 Receptor Antagonist for the Treatment of Bronchiolitis Obliterans

Post author:Patient Worthy Contributor
Post published:August 20, 2018
Post category:Rare Disease

According to a story from Business Wire, the biopharmaceutical company Onspira Therapeutics recently announced that its investigational therapy OSP-101 was recently granted Orphan Drug designation by the US Food and…

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Experimental Duchenne Muscular Dystrophy Drug Gets Multiple Designations From the FDA

Post author:James Moore
Post published:August 20, 2018
Post category:Duchenne Muscular Dystrophy Muscular Dystrophy

According to a story from Globe Newswire, the biotechnology company Wave Life Sciences recently announced that its investigational product WVE-210201 has received both Rare Pediatric disease designation and Orphan Drug…

rawpixel / Pixabay

The FDA Wants to Listen to Patient Voices in Medical Development and Regulation

Post author:Anna Hewitt
Post published:August 20, 2018
Post category:Rare Disease

The US Food and Drug Administration (FDA) has released a statement outlining its plans to promote patient voices in the development and regulation of medical products. You can find more…

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Warnings From the FDA go Largely Unnoticed by State Medical Boards

Post author:James Moore
Post published:August 20, 2018
Post category:Rare Disease

According to a story from USA Today, despite numerous warning letters sent from the US Food and Drug Administration to the offices of doctors and other medical professionals across the…

Skitterphoto / Pixabay

Artificial Intelligence Can Accurately Recommend Patient Referrals For Eye Conditions

Post author:Anna Hewitt
Post published:August 20, 2018
Post category:Rare Disease

Researchers have found that an artificial intelligence (AI) system is able to recommend patient referrals for over fifty eye conditions as accurately as world-leading doctors. The project is part of…

For Low-Risk Thyroid Cancer, Doctors Shouldn’t Use the Word “Cancer”

Post author:Athena Lee
Post published:August 20, 2018
Post category:Thyroid Cancer

According to The Guardian, some researchers believe that the term "cancer" should be omitted from some medical diagnoses. Among these diagnoses include those for small thyroid cancer, low and intermediate…

ulleo / Pixabay

Planting the Seeds of Sarcoma Awareness

Post author:James Moore
Post published:August 20, 2018
Post category:Rare Disease Soft Tissue Sarcoma

According to a story from Deseret News, sarcoma patients at the Huntsman Cancer Institute are planting sunflowers as a way to spread awareness about sarcoma, a rare and aggressive form…

Important Questions to Ask After a Breast Cancer Diagnosis

Post author:Athena Lee
Post published:August 20, 2018
Post category:Metastatic Breast Cancer

According to the Dover Post, there are a few crucial questions to ask your doctor upon being diagnosed with breast cancer. By asking these crucial questions, patients will be…

Pettycon / Pixabay

The FDA Has Approved the First Generic Version of EpiPen

Post author:Anna Hewitt
Post published:August 20, 2018
Post category:Rare Disease

The United States FDA has approved the first generic version of EpiPen and EpiPen Jr (epinephrine). The approval was granted to Teva Pharmaceuticals USA, who will now be able to…

LaCasadeGoethe / Pixabay

Two Companies are Collaborating to Develop an Investigational Drug for Epidermolysis Bullosa

Post author:Anna Hewitt
Post published:August 20, 2018
Post category:Epidermolysis Bullosa

Two companies, GtreeBNT and YuYang DNU, will collaborate in a joint venture to develop the investigational drug RGN-137 for the treatment of epidermolysis bullosa. For more details, you can read…

FDA Grants Orphan Drug Designation to Onspira Therapeutics’ Investigational Interleukin-1 Receptor Antagonist for the Treatment of Bronchiolitis Obliterans

Experimental Duchenne Muscular Dystrophy Drug Gets Multiple Designations From the FDA

The FDA Wants to Listen to Patient Voices in Medical Development and Regulation

Warnings From the FDA go Largely Unnoticed by State Medical Boards

Artificial Intelligence Can Accurately Recommend Patient Referrals For Eye Conditions

For Low-Risk Thyroid Cancer, Doctors Shouldn’t Use the Word “Cancer”

Planting the Seeds of Sarcoma Awareness

Important Questions to Ask After a Breast Cancer Diagnosis

The FDA Has Approved the First Generic Version of EpiPen

Two Companies are Collaborating to Develop an Investigational Drug for Epidermolysis Bullosa

The Let’s Chat CAR T One-on-One Mentor Program: Speaking with Someone Who Understands What You Are Going Through

“Shades of Psoriasis”: Plaque Psoriasis and Sharing Your Story

Understanding RSV: Why Combatting Ethnic and Age-Related Health Disparities Could Improve Outcomes

We Need Equity and Diversity Within Rare Disease Research

DNA in Color: How Ronya Nelson is Working to Close the Diversity Gap in Genetics - Part 1

Bridging the Diversity Gap in Healthcare

Congratulations to the 2023 Recipients of the Diversity in Lupus Research Awards!

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