The United States government has awarded a grant of over $4 million to fund research into genetic mitochondrial diseases. The three-year grant was given to the Children’s Hospital of Philadelphia…
According to a story from uk.news.yahoo.com, Sammy Basso is 22 years old, and for him, it is a miracle. That is because Sammy is living with the rare genetic disorder…
According to a story from Hematology Times, a recent phase 2 study found that a three-part combination treatment could be a valuable treatment option for patients with chronic lymphocytic leukemia.…
TMI Alert! Pooping, or lack thereof, deserves its own book. Constipation. Hemorrhoids. Ugh! Nothing helped. Over the counter remedies, enemas, plenty of fluids, a diet high in fiber. I tried…
A recent study, carried out by researchers from the National Cancer Institute (part of the NIH) and several other universities, outlines a potential new method of predicting whether immune checkpoint…
According to a story from Multiple Sclerosis News Today, a recent case report suggests that switching from the immunotherapy drug Gilenya to another immunotherapy called Lemtrada could cause a severe…
Despite my misfortune, I still live life to the fullest I can. At three years of age, I was diagnosed with a rare disease, which initially had little impact on…
Pfizer has released the primary results from the Phase 3 clinical trial of tafamidis, an investigational drug being researched as a potential treatment for transthyretin amyloid cardiomyopathy. For more…
According to a story from Newswise, the results of a phase 3 clinical trial suggest that the medication tafamidis could substantially reduce the risk of hospitalization or death for patients…
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