New Clinical Trial Application for Alpha-1 Antitrypsin Deficiency-Associated Liver Disease Submitted in Sweden

Dicerna Pharmaceuticals has just announced that they have submitted a Clinical Trial Authorization application for their investigational therapy DCR-A1AT. This application has been submitted to the Swedish Medical Products Agency…

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Family That Lost Newborn to Trisomy 18 Hosting Fundraiser to Give Back to Hospice Center that Supported Them
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Family That Lost Newborn to Trisomy 18 Hosting Fundraiser to Give Back to Hospice Center that Supported Them

According to a publication from the Basingstoke Gazette, a Basingstoke family is raising money for the children's hospice center that supported them through the loss of a child. Jessica and…

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Company Starts up Late Stage Trial Testing Experimental WHIM Syndrome Treatment
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Company Starts up Late Stage Trial Testing Experimental WHIM Syndrome Treatment

According to a story from BioPortfolio, the biopharmaceutical company X4 Pharmaceuticals, Inc. has recently initiated a phase 3 clinical trial that is testing its current lead product candidate mavorixafor. This…

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