According to a story from Healio, a recent presentation featured at the FH Foundation Global Summit was a stark reminder of the need for improved treatment for patients with familial…
Copyscape score: 4% A common symptom of Rett Syndrome is apnea, which is a difficulty in breathing. This apnea has been a symptom that has had no treatment for a…
According to a story from pharmaphorum.com, the drug company Genfit has recently released data from a study which was testing the effectiveness of a new approach for the diagnosis of…
According to a story from Medscape, the European Medicines Agency's Committee for Medicinal Products for Human Use (CHMP) has recently issued a positive recommendation for the drug osilodrostat. This is…
There have been extreme improvements in genetic engineering over the past fifty years since it was pioneered in the 1970s. It has been used for the treatment of various…
According to a story from Soweto Urban, mother Lebohang Leuta is no stranger to the challenges that come with raising and taking care of a child with a chronic rare…
According to a story from EurekAlert!, a collaborative study headed by researchers from Yale University has furthered the understanding of the mechanisms and progression of fibrosis (scarring) in patients with…
According to a story from BioSpace, the gene therapy companies Sarepta Therapeutics, Inc. and StrideBio, Inc. have recently announced the completion of a licensing and collaboration agreement that could lead…
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