A study published in the Journal of Clinical Oncology has detailed the benefits of different forms of treatment for pediatric patients with adrenocortical carcinoma. These researchers particularly looked at what treatments…
Ryan Alam was diagnosed with mitochondrial-membrane protein-associated neurodegeneration (MPAN), a rare form of neurodegeneration with brain iron accumulation (NBIA), but he hasn't let these conditions slow him down. He has just…
Retinitis Pigmentosa Retinitis Pigmentosa is a rare condition which progressively causes vision loss. Genetic lesions which first affect the rod photoreceptors first cause vision loss at night. Next, cone photoreceptors are…
Gene therapy is a recent development in the industry, and it is one that has brought hope to many people who live with a genetic condition without a viable treatment…
VISEN Pharmaceuticals has recently announced that enrollment has been completed for their Phase 3 clinical trial examining the safety and efficacy of TransCon hGH compared to daily rhGH in patients…
Medical research is crucial to expanding an understanding of certain conditions, which ultimately leads to improved diagnostic and treatment options, and more social awareness. In a recent press release, CurePSP…
How effective is guselkumab, a human monoclonal antibody, at treating patients with psoriatic arthritis (PsA)? According to post-hoc data analysis from two clinical trials, the therapy was relatively effective.…
According to a story from thehansindia.com, 47 year old Xaverine Mukabaranga of Rwanda, Africa, checked herself into Manipal Hospitals. She reported symptoms of persistent chest pain affected her left side.…
According to a news release from April 2021, a new partnership is working to improve the commercialization of rare disease drugs for patients in China. Together, rare disease therapeutics company…
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