In 2019, Connor Dobbyn, now 13, was diagnosed with Sanfilippo syndrome type C, also known as mucopolysaccharidosis III (MPS III). After his diagnosis, his parents came to recognize that there…
When we are injured, new cells flow to the injury site and replace the body’s damaged cells. This process is called “cell migration.” According to a recent article in Science…
According to a recent article, a young girl’s struggle with mitochondrial disease has led to a mitochondrial donation bill finally being brought to vote in Parliament in Australia. Mitochondrial Diseases…
European patients with recurrent or advanced endometrial carcinoma have a new treatment option, as the European Commission (EC) has approved KEYTRUDA plus LENVIMA. Approval is specifically for adult patients whose…
A recent article in Medical Life Sciences alerts physicians to be aware of a deadly skin cancer. It is called cytotoxic cutaneous T-cell lymphoma (CTCL). According to an article in…
Doctor Jeffrey Miner, who is a member of the Alport Syndrome Foundation's (ASF) Scientific Advisory Research Network, was just awarded a Ro1 grant worth 2.25 million dollars for his research in Alport…
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