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Daily Archives: September 28, 2022

Home » Archives for September 28, 2022
GNS561 Earns Orphan Drug Designation for Cholangiocarcinoma
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GNS561 Earns Orphan Drug Designation for Cholangiocarcinoma

  • Post author:Jessica Lynn
  • Post published:September 28, 2022
  • Post category:Cholangiocarcinoma

  According to an article from Cancer Network, the U.S. Food and Drug Administration (FDA) recently granted Orphan Drug designation to second-line GNS561 (ezurpimtrostrat) for cholangiocarcinoma (bile duct cancer).  In…

Continue Reading GNS561 Earns Orphan Drug Designation for Cholangiocarcinoma
Science Simplified: What Are Proteins And How Can You Look at Them?
source: pixabay.com

Science Simplified: What Are Proteins And How Can You Look at Them?

  • Post author:Patient Worthy Contributor
  • Post published:September 28, 2022
  • Post category:Rare Disease/SLC13A5 deficiency

Want to learn about scientific topics without needing a PhD? Check out the Science Simplified blog from TESS Research Foundation! Dr. Tanya Brown, PhD, works with researchers to make science…

Continue Reading Science Simplified: What Are Proteins And How Can You Look at Them?
Woman Shares her Experience with FIRES and Recovery
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Woman Shares her Experience with FIRES and Recovery

  • Post author:Jessica Lynn
  • Post published:September 28, 2022
  • Post category:febrile infection-related epilepsy syndrome

At 20 years old, Grace Hinchman was - for all intents and purposes - a happy and healthy young adult. Grace was studying Business at Loyola University Chicago and playing…

Continue Reading Woman Shares her Experience with FIRES and Recovery
7-Year-Old Diagnosed With Diffuse Midline Glioma, a Rare Brain Cancer

7-Year-Old Diagnosed With Diffuse Midline Glioma, a Rare Brain Cancer

  • Post author:Rose Duesterwald
  • Post published:September 28, 2022
  • Post category:Diffuse Midline Glioma

Seven-year-old Rydder Ames of Hamilton, Ohio began having symptoms five months ago. His mother, Krista Steven took him to the ER after a week-long headache followed by a loss of…

Continue Reading 7-Year-Old Diagnosed With Diffuse Midline Glioma, a Rare Brain Cancer
Could High-Dose Tisagenlecleucel Increase B-Cell ALL Survival?
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Could High-Dose Tisagenlecleucel Increase B-Cell ALL Survival?

  • Post author:Jessica Lynn
  • Post published:September 28, 2022
  • Post category:Acute lymphoblastic leukemia

How does CAR T-cell therapy affect an enhanced anti-leukemia effect? Could higher doses influence toxicity or change patient outcomes? According to an article in the Pharmacy Times, researchers sought to…

Continue Reading Could High-Dose Tisagenlecleucel Increase B-Cell ALL Survival?

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