Experimental Limb-Girdle Muscular Dystrophy Drug May Have Path to Accelerated Approval
source: shutterstock.com

Experimental Limb-Girdle Muscular Dystrophy Drug May Have Path to Accelerated Approval

According to a story from BioPharma Dive, the drug company BridgeBio has been working on the development of a new treatment for limb-girdle muscular dystrophy, a rare disease. At the…

Continue Reading Experimental Limb-Girdle Muscular Dystrophy Drug May Have Path to Accelerated Approval
Rare Classroom: WHIM Syndrome
source: shutterstock

Rare Classroom: WHIM Syndrome

Welcome to the Rare Classroom, a new series from Patient Worthy. Rare Classroom is designed for the curious reader who wants to get informed on some of the rarest, most…

Continue Reading Rare Classroom: WHIM Syndrome