Ionis Pharmaceuticals Announces Positive Results in Familial Chylomicronemia Syndrome
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Ionis Pharmaceuticals Announces Positive Results in Familial Chylomicronemia Syndrome

  This week Ionis Pharmaceuticals, Inc. issued a press release via PRNewswire announcing topline Phase 3 results for its Balance study of olezarsen. The study ( NCT04568434 ) enrolled people with…

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Rare Community Profiles: Dr. Brian Koffman Discusses the Complexities of Immunization for People with CLL/SLL
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Rare Community Profiles: Dr. Brian Koffman Discusses the Complexities of Immunization for People with CLL/SLL

Rare Community Profiles     Rare Community Profiles is a Patient Worthy article series of long-form interviews featuring various stakeholders in the rare disease community, such as patients, their families,…

Continue Reading Rare Community Profiles: Dr. Brian Koffman Discusses the Complexities of Immunization for People with CLL/SLL